GENE-THERAPY FOR DUCHENNE DYSTROPHY

被引:7
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ENGEL, AG
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10.1002/ana.410340103
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R74 [神经病学与精神病学];
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页码:3 / 4
页数:2
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共 15 条
[1]   HUMAN DYSTROPHIN EXPRESSION IN MDX MICE AFTER INTRAMUSCULAR INJECTION OF DNA CONSTRUCTS [J].
ACSADI, G ;
DICKSON, G ;
LOVE, DR ;
JANI, A ;
WALSH, FS ;
GURUSINGHE, A ;
WOLFF, JA ;
DAVIES, KE .
NATURE, 1991, 352 (6338) :815-818
[2]   NORMAL DYSTROPHIN TRANSCRIPTS DETECTED IN DUCHENNE MUSCULAR-DYSTROPHY PATIENTS AFTER MYOBLAST TRANSPLANTATION [J].
GUSSONI, E ;
PAVLATH, GK ;
LANCTOT, AM ;
SHARMA, KR ;
MILLER, RG ;
STEINMAN, L ;
BLAU, HM .
NATURE, 1992, 356 (6368) :435-438
[3]   LYSIS OF MYOTUBES BY ALLOREACTIVE CYTOTOXIC T-CELLS AND NATURAL-KILLER-CELLS - RELEVANCE TO MYOBLAST TRANSPLANTATION [J].
HOHLFELD, R ;
ENGEL, AG .
JOURNAL OF CLINICAL INVESTIGATION, 1990, 86 (01) :370-374
[4]  
HOHLFELD R, 1990, AM J PATHOL, V136, P503
[5]   HUMAN MYOBLAST TRANSPLANTATION - PRELIMINARY-RESULTS OF 4 CASES [J].
HUARD, J ;
BOUCHARD, JP ;
ROY, R ;
MALOUIN, F ;
DANSEREAU, G ;
LABRECQUE, C ;
ALBERT, N ;
RICHARDS, CL ;
LEMIEUX, B ;
TREMBLAY, JP .
MUSCLE & NERVE, 1992, 15 (05) :550-560
[6]   MYOBLAST TRANSFER IN DUCHENNE MUSCULAR-DYSTROPHY [J].
KARPATI, G ;
AJDUKOVIC, D ;
ARNOLD, D ;
GLEDHILL, RB ;
GUTTMANN, R ;
HOLLAND, P ;
KOCH, PA ;
SHOUBRIDGE, E ;
SPENCE, D ;
VANASSE, M ;
WATTERS, GV ;
ABRAHAMOWICZ, M ;
DUFF, C ;
WORTON, RG .
ANNALS OF NEUROLOGY, 1993, 34 (01) :8-17
[7]  
KARPATI G, 1989, AM J PATHOL, V135, P27
[8]  
Law P K, 1992, Cell Transplant, V1, P235
[9]   NORMAL MYOBLAST INJECTIONS PROVIDE GENETIC TREATMENT FOR MURINE DYSTROPHY [J].
LAW, PK ;
GOODWIN, TG ;
WANG, MG .
MUSCLE & NERVE, 1988, 11 (06) :525-533
[10]   THE BASIC SCIENCE OF GENE-THERAPY [J].
MULLIGAN, RC .
SCIENCE, 1993, 260 (5110) :926-932