共 48 条
CYSTIC-FIBROSIS GENE-THERAPY
被引:24
作者:

COLLEDGE, WH
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV CAMBRIDGE, DEPT GENET, CAMBRIDGE CB2 1QR, CAMBS, ENGLAND UNIV CAMBRIDGE, DEPT GENET, CAMBRIDGE CB2 1QR, CAMBS, ENGLAND
机构:
[1] UNIV CAMBRIDGE, DEPT GENET, CAMBRIDGE CB2 1QR, CAMBS, ENGLAND
关键词:
D O I:
10.1016/0959-437X(94)90037-X
中图分类号:
Q2 [细胞生物学];
学科分类号:
071009 ;
090102 ;
摘要:
A variety of cystic fibrosis gene therapy approaches based on viral (adenovirus, retrovirus, and adeno-associated virus) and non-viral (liposomes and receptor-mediated endocytosis) routes are currently being assessed for safety and efficacy. Of these, the trials involving liposomal and adenoviral vectors are the most advanced, as both have been shown to correct the cystic fibrosis Cl- conductance defect in vivo.
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页码:466 / 471
页数:6
相关论文
共 48 条
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NONINVASIVE LIPOSOME-MEDIATED GENE DELIVERY CAN CORRECT THE ION-TRANSPORT DEFECT IN CYSTIC-FIBROSIS MUTANT MICE
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SMITH, SN
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MUNKONGE, FM
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JEFFERY, PK
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GEDDES, DM
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HART, SL
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WILLIAMSON, R
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FASOLD, KI
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ALTON, EWFW
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

MIDDLETON, PG
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

CAPLEN, NJ
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

SMITH, SN
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

STEEL, DM
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

MUNKONGE, FM
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

JEFFERY, PK
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

GEDDES, DM
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

HART, SL
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

WILLIAMSON, R
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

FASOLD, KI
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

MILLER, AD
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

DICKINSON, P
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

STEVENSON, BJ
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

MCLACHLAN, G
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

DORIN, JR
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND

PORTEOUS, DJ
论文数: 0 引用数: 0
h-index: 0
机构: NATL HEART & LUNG INST,DEPT LUNG PATHOL,LONDON SW3 6LR,ENGLAND
[2]
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BAYLE, JY
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,UNC LINEBERGER COMPREHENS CANC CTR,CB 7295,139 LINEBERGER,CHAPEL HILL,NC 27599

JOHNSON, LG
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,UNC LINEBERGER COMPREHENS CANC CTR,CB 7295,139 LINEBERGER,CHAPEL HILL,NC 27599

STGEORGE, JA
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,UNC LINEBERGER COMPREHENS CANC CTR,CB 7295,139 LINEBERGER,CHAPEL HILL,NC 27599

BOUCHER, RC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,UNC LINEBERGER COMPREHENS CANC CTR,CB 7295,139 LINEBERGER,CHAPEL HILL,NC 27599

OLSEN, JC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,UNC LINEBERGER COMPREHENS CANC CTR,CB 7295,139 LINEBERGER,CHAPEL HILL,NC 27599
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BORISLAWRIE, KA
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h-index: 0
机构:
UNIV WISCONSIN, MADISON, WI 53706 USA UNIV WISCONSIN, MADISON, WI 53706 USA

TEMIN, HM
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV WISCONSIN, MADISON, WI 53706 USA UNIV WISCONSIN, MADISON, WI 53706 USA
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BRIGHAM, KL
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

MEYRICK, B
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

CHRISTMAN, B
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

MAGNUSON, M
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

KING, G
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

BERRY, LC
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232
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1993, 8 (02)
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BRIGHAM, KL
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h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

MEYRICK, B
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

CHRISTMAN, B
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

CONARY, JT
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

KING, G
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

BERRY, LC
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232

MAGNUSON, MA
论文数: 0 引用数: 0
h-index: 0
机构: VANDERBILT UNIV,MED CTR,SCH MED,DEPT PATHOL,NASHVILLE,TN 37232
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CLARKE, LL
论文数: 0 引用数: 0
h-index: 0
机构:
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GRUBB, BR
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514 UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514

GABRIEL, SE
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514 UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514

SMITHIES, O
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514 UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514

KOLLER, BH
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514 UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514

BOUCHER, RC
论文数: 0 引用数: 0
h-index: 0
机构:
UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514 UNIV N CAROLINA,DEPT MED,DIV PULM DIS,CHAPEL HILL,NC 27514
[7]
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COLLEDGE, WH
论文数: 0 引用数: 0
h-index: 0
机构:
ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND

RATCLIFF, R
论文数: 0 引用数: 0
h-index: 0
机构:
ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND

FOSTER, D
论文数: 0 引用数: 0
h-index: 0
机构:
ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND

WILLIAMSON, R
论文数: 0 引用数: 0
h-index: 0
机构:
ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND

EVANS, MJ
论文数: 0 引用数: 0
h-index: 0
机构:
ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND ST MARYS HOSP,SCH MED,DEPT BIOCHEM & MOLEC GENET,LONDON W2 1PG,ENGLAND
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COUTELLE, C
论文数: 0 引用数: 0
h-index: 0

CAPLEN, N
论文数: 0 引用数: 0
h-index: 0

HART, S
论文数: 0 引用数: 0
h-index: 0

HUXLEY, C
论文数: 0 引用数: 0
h-index: 0

WILLIAMSON, R
论文数: 0 引用数: 0
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CURIEL, DT
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

WAGNER, E
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

COTTEN, M
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

BIRNSTIEL, ML
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

AGARWAL, S
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

LI, CM
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

LOECHEL, S
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599

HU, PC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT PEDIAT,CHAPEL HILL,NC 27599
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BOUCHER, RC
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AMERICAN JOURNAL OF RESPIRATORY CELL AND MOLECULAR BIOLOGY,
1992, 6 (03)
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CURIEL, DT
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599

AGARWAL, S
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599

ROMER, MU
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599

WAGNER, E
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599

COTTEN, M
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599

BIRNSTIEL, ML
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599

BOUCHER, RC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV N CAROLINA,DEPT MED,CHAPEL HILL,NC 27599