2 STEPS CLOSER TO GENE-THERAPY FOR CYSTIC-FIBROSIS

被引:3
作者
CUTTING, GR
机构
[1] JOHNS HOPKINS UNIV HOSP,SCH MED,DEPT PEDIAT,BALTIMORE,MD 21205
[2] JOHNS HOPKINS UNIV HOSP,SCH MED,DEPT MED,BALTIMORE,MD 21205
关键词
D O I
10.1038/ng0992-4
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
[No abstract available]
引用
收藏
页码:4 / 5
页数:2
相关论文
共 11 条
  • [1] CHU CS, IN PRESS J CLIN INVE
  • [2] IMMUNOCYTOCHEMICAL LOCALIZATION OF THE CYSTIC-FIBROSIS GENE-PRODUCT CFTR
    CRAWFORD, I
    MALONEY, PC
    ZEITLIN, PL
    GUGGINO, WB
    HYDE, SC
    TURLEY, H
    GATTER, KC
    HARRIS, A
    HIGGINS, CF
    [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1991, 88 (20) : 9262 - 9266
  • [3] DEFECTIVE REGULATION OF OUTWARDLY RECTIFYING CL- CHANNELS BY PROTEIN KINASE-A CORRECTED BY INSERTION OF CFTR
    EGAN, M
    FLOTTE, T
    AFIONE, S
    SOLOW, R
    ZEITLIN, PL
    CARTER, BJ
    GUGGINO, WB
    [J]. NATURE, 1992, 358 (6387) : 581 - 584
  • [4] EFFICIENCY OF GENE-TRANSFER FOR RESTORATION OF NORMAL AIRWAY EPITHELIAL FUNCTION IN CYSTIC-FIBROSIS
    JOHNSON, LG
    OLSEN, JC
    SARKADI, B
    MOORE, KL
    SWANSTROM, R
    BOUCHER, RC
    [J]. NATURE GENETICS, 1992, 2 (01) : 21 - 25
  • [5] MISLOCALIZATION OF DELTA-F508 CFTR IN CYSTIC-FIBROSIS SWEAT GLAND
    KARTNER, N
    AUGUSTINAS, O
    JENSEN, TJ
    NAISMITH, AL
    RIORDAN, JR
    [J]. NATURE GENETICS, 1992, 1 (05) : 321 - 327
  • [6] KRISTIDIS P, 1992, AM J HUM GENET, V50, P1178
  • [7] LOCALIZATION OF THE CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR IN PANCREAS
    MARINO, CR
    MATOVCIK, LM
    GORELICK, FS
    COHN, JA
    [J]. JOURNAL OF CLINICAL INVESTIGATION, 1991, 88 (02) : 712 - 716
  • [8] Plopper C. G., 1992, TREATISE PULMONARY T, V1
  • [9] INVIVO TRANSFER OF THE HUMAN CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR GENE TO THE AIRWAY EPITHELIUM
    ROSENFELD, MA
    YOSHIMURA, K
    TRAPNELL, BC
    YONEYAMA, K
    ROSENTHAL, ER
    DALEMANS, W
    FUKAYAMA, M
    BARGON, J
    STIER, LE
    STRATFORDPERRICAUDET, L
    PERRICAUDET, M
    GUGGINO, WB
    PAVIRANI, A
    LECOCQ, JP
    CRYSTAL, RG
    [J]. CELL, 1992, 68 (01) : 143 - 155
  • [10] EXPRESSION OF THE CYSTIC-FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR GENE IN THE RESPIRATORY-TRACT OF NORMAL INDIVIDUALS AND INDIVIDUALS WITH CYSTIC-FIBROSIS
    TRAPNELL, BC
    CHU, CS
    PAAKKO, PK
    BANKS, TC
    YOSHIMURA, K
    FERRANS, VJ
    CHERNICK, MS
    CRYSTAL, RG
    [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1991, 88 (15) : 6565 - 6569