ASGCT and JS']JSGT Joint Position Statement on Human Genomic Editing

被引：42

作者：

Friedmann, Theodore ^{[1
]}

Jonlin, Erica C. ^{[2
]}

King, Nancy M. P. ^{[3
]}

Torbett, Bruce E. ^{[4
]}

Wivel, Nelson A. ^{[5
]}

Kaneda, Yasufumi ^{[6
]}

Sadelain, Michel ^{[7
]}

机构：

[1] Univ Calif San Diego, Sch Med, Inst Genom Med, Dept Pediat, La Jolla, CA 92093 USA

[2] Univ Washington, Sch Med, Dept Med, Div Hematol, Seattle, WA 98195 USA

[3] Wake Forest Sch Med, Dept Social Sci & Hlth Policy, Winston Salem, NC USA

[4] Scripps Res Inst, Dept Mol & Expt Med, Mol & Cellular Therapy, La Jolla, CA 92037 USA

[5] Univ Penn, Philadelphia, PA 19104 USA

[6] Osaka Univ, Grad Sch Med, Div Gene Therapy, Suita, Osaka, Japan

[7] Mem Sloan Kettering Canc Ctr, Ctr Cell Engn, New York, NY 10021 USA

来源：

MOLECULAR THERAPY | 2015年 / 23卷 / 08期

关键词：

DYSTROPHIC EPIDERMOLYSIS-BULLOSA; FIBROBLAST CELL THERAPY; VEHICLE-CONTROLLED TRIAL; BONE-MARROW; VII COLLAGEN; SKIN; TRANSPLANTS;

D O I：

10.1038/mt.2015.118

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：1282 / 1284

页数：3

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