Preemptive therapy for genetic disease

被引:10
作者
Blau, CA [1 ]
Stamatoyannopoulos, G [1 ]
机构
[1] UNIV WASHINGTON,DIV MED GENET,SEATTLE,WA 98195
关键词
D O I
10.1038/nm0296-161
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
引用
收藏
页码:161 / 162
页数:2
相关论文
共 7 条
[1]  
BUCKLEY RH, 1986, J IMMUNOL, V136, P2398
[2]  
COWAN MJ, 1994, AM J PEDIAT HEMATOL, V16, P35
[3]  
Flake A. W., 1995, Blood, V86, p125A
[4]   ANALYSIS OF BETA-GLOBIN MUTATIONS SHOWS STABLE MIXED CHIMERISM IN PATIENTS WITH THALASSEMIA AFTER BONE-MARROW TRANSPLANTATION [J].
KAPELUSHNIK, J ;
OR, R ;
FILON, D ;
NAGLER, A ;
CIVIDALLI, G ;
AKER, M ;
NAPARSTEK, E ;
SLAVIN, S ;
OPPENHEIM, A .
BLOOD, 1995, 86 (08) :3241-3246
[5]   MARROW TRANSPLANTATION IN PATIENTS WITH THALASSEMIA RESPONSIVE TO IRON CHELATION-THERAPY [J].
LUCARELLI, G ;
GALIMBERTI, M ;
POLCHI, P ;
ANGELUCCI, E ;
BARONCIANI, D ;
GIARDINI, C ;
ANDREANI, M ;
AGOSTINELLI, F ;
ALBERTINI, F ;
CLIFT, RA .
NEW ENGLAND JOURNAL OF MEDICINE, 1993, 329 (12) :840-844
[6]  
NESCI S, 1992, BONE MARROW TRANSPL, V10, P143
[7]   INTERLEUKIN-2 RECEPTOR GAMMA CHAIN MUTATION RESULTS IN X-LINKED SEVERE COMBINED IMMUNODEFICIENCY IN HUMANS [J].
NOGUCHI, M ;
YI, HF ;
ROSENBLATT, HM ;
FILIPOVICH, AH ;
ADELSTEIN, S ;
MODI, WS ;
MCBRIDE, OW ;
LEONARD, WJ .
CELL, 1993, 73 (01) :147-157