Antisense-Mediated Exon Skipping: Networking to Meet Opportunities and to Overcome Challenges

被引：11

作者：

Aartsma-Rus, Annemieke ^{[1
]}

机构：

[1] Leiden Univ, Med Ctr, Dept Human Genet, NL-2333 ZA Leiden, Netherlands

来源：

NUCLEIC ACID THERAPEUTICS | 2014年 / 24卷 / 01期

关键词：

OLIGONUCLEOTIDES;

D O I：

10.1089/nat.2014.1500

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

引用

页码：1 / 3

页数：3

共 10 条

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[5] Peptide Conjugation of 2′-O-methyl Phosphorothioate Antisense Oligonucleotides Enhances Cardiac Uptake and Exon Skipping in mdx Mice [J].

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