Adeno-associated virus-mediated gene transfer of factor IX for treatment of hemophilia B by gene therapy

被引：25

作者：

Herzog, RW

High, KA

机构：

[1] Childrens Hosp Philadelphia, Div Hematol, Abramson Res Ctr 310A, Philadelphia, PA 19104 USA

[2] Univ Penn, Med Ctr, Dept Pediat, Philadelphia, PA 19104 USA

[3] Univ Penn, Med Ctr, Dept Pathol, Philadelphia, PA 19104 USA

来源：

THROMBOSIS AND HAEMOSTASIS | 1999年 / 82卷 / 02期

关键词：

D O I：

10.1055/s-0037-1615877

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：540 / 546

页数：7

共 48 条

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