学术探索
学术期刊
新闻热点
数据分析
智能评审
立即登录
Toward gene therapy for hemophilia A with novel adenoviral vectors: successes and limitations in canine models
被引:12
作者
:
Arruda, VR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Dept Pediat, Philadelphia, PA 19104 USA
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Dept Pediat, Philadelphia, PA 19104 USA
Arruda, VR
[
1
]
机构
:
[1]
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Dept Pediat, Philadelphia, PA 19104 USA
来源
:
JOURNAL OF THROMBOSIS AND HAEMOSTASIS
|
2006年
/ 4卷
/ 06期
关键词
:
D O I
:
10.1111/j.1538-7836.2006.01964.x
中图分类号
:
R5 [内科学];
学科分类号
:
1002 ;
100201 ;
摘要
:
引用
收藏
页码:1215 / 1217
页数:3
相关论文
共 16 条
[1]
FACTOR-VIII GENE INVERSIONS IN SEVERE HEMOPHILIA-A - RESULTS OF AN INTERNATIONAL CONSORTIUM STUDY
ANTONARAKIS, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
ANTONARAKIS, SE
ROSSITER, JP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
ROSSITER, JP
YOUNG, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
YOUNG, M
HORST, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
HORST, J
DEMOERLOOSE, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
DEMOERLOOSE, P
SOMMER, SS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SOMMER, SS
KETTERLING, RP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KETTERLING, RP
KAZAZIAN, HH
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KAZAZIAN, HH
NEGRIER, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
NEGRIER, C
VINCIGUERRA, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VINCIGUERRA, C
GITSCHIER, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GITSCHIER, J
GOOSSENS, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GOOSSENS, M
GIRODON, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GIRODON, E
GHANEM, N
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GHANEM, N
PLASSA, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PLASSA, F
LAVERGNE, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LAVERGNE, JM
VIDAUD, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VIDAUD, M
COSTA, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
COSTA, JM
LAURIAN, Y
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LAURIAN, Y
LIN, SW
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LIN, SW
LIN, SR
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LIN, SR
SHEN, MC
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SHEN, MC
LILLICRAP, D
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LILLICRAP, D
TAYLOR, SAM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
TAYLOR, SAM
WINDSOR, S
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
WINDSOR, S
VALLEIX, SV
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VALLEIX, SV
NAFA, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
NAFA, K
SULTAN, Y
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SULTAN, Y
DELPECH, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
DELPECH, M
VNENCAKJONES, CL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VNENCAKJONES, CL
PHILLIPS, JA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PHILLIPS, JA
LJUNG, RCR
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LJUNG, RCR
KOUMBARELIS, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KOUMBARELIS, E
GIALERAKI, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GIALERAKI, A
MANDALAKI, T
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
MANDALAKI, T
JENKINS, PV
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
JENKINS, PV
COLLINS, PW
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
COLLINS, PW
PASI, KJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PASI, KJ
GOODEVE, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GOODEVE, A
PEAKE, I
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PEAKE, I
PRESTON, FE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PRESTON, FE
SCHWARTZ, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SCHWARTZ, M
SCHEIBEL, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SCHEIBEL, E
INGERSLEV, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
INGERSLEV, J
COOPER, DN
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
COOPER, DN
MILLAR, DS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
MILLAR, DS
KAKKAR, VV
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KAKKAR, VV
GIANNELLI, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GIANNELLI, F
NAYLOR, JA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
NAYLOR, JA
TIZZANO, EF
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
TIZZANO, EF
[J].
BLOOD,
1995,
86
(06)
: 2206
-
2212
[2]
Helper-dependent adenoviral vectors mediate therapeutic factor VIII expression for several months with minimal accompanying toxicity in a canine model of severe hemophilia A
Brown, BD
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Brown, BD
Shi, CX
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Shi, CX
Powell, S
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Powell, S
Hurlbut, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Hurlbut, D
Graham, FL
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Graham, FL
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Lillicrap, D
[J].
BLOOD,
2004,
103
(03)
: 804
-
810
[3]
Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors
Chuah, MKL
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Chuah, MKL
Schiedner, G
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Schiedner, G
Thorrez, L
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Thorrez, L
Brown, B
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Brown, B
Johnston, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Johnston, M
Gillijns, V
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Gillijns, V
Hertel, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Hertel, S
Van Rooijen, N
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Van Rooijen, N
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Lillicrap, D
Collen, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Collen, D
VandenDriessche, T
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
VandenDriessche, T
Kochanek, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Kochanek, S
[J].
BLOOD,
2003,
101
(05)
: 1734
-
1743
[4]
A gene-deleted adenoviral vector results in phenotypic correction of canine hemophilia B without liver toxicity or thrombocytopenia
Ehrhardt, A
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Ehrhardt, A
Xu, H
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Xu, H
Dillow, AM
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Dillow, AM
Bellinger, DA
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Bellinger, DA
Nichols, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Nichols, TC
Kay, MA
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Kay, MA
[J].
BLOOD,
2003,
102
(07)
: 2403
-
2411
[5]
Germline alteration by gene therapy: assessing and reducing the risks
Gordon, JW
论文数:
0
引用数:
0
h-index:
0
机构:
Mt Sinai Med Ctr, Dept Neurobiol, New York, NY 10029 USA
Gordon, JW
[J].
MOLECULAR MEDICINE TODAY,
1998,
4
(11):
: 468
-
470
[6]
Gene therapy for hemophilia: an imperative to succeed
Hough, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Hough, C
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Lillicrap, D
[J].
JOURNAL OF THROMBOSIS AND HAEMOSTASIS,
2005,
3
(06)
: 1195
-
1205
[7]
Aberrant splicing and premature termination of transcription of the FVIII gene as a cause of severe canine hemophilia A: Similarities with the intron 22 inversion mutation in human hemophilia
Hough, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Hough, C
Kamisue, S
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Kamisue, S
Cameron, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Cameron, C
Notley, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Notley, C
Tinlin, S
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Tinlin, S
Giles, A
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Giles, A
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Lillicrap, D
[J].
THROMBOSIS AND HAEMOSTASIS,
2002,
87
(04)
: 659
-
665
[8]
Factor VIII alloantibodies in hemophilia
Jacquemin, MG
论文数:
0
引用数:
0
h-index:
0
机构:
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Jacquemin, MG
Saint-Remy, JMR
论文数:
0
引用数:
0
h-index:
0
机构:
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Saint-Remy, JMR
[J].
CURRENT OPINION IN HEMATOLOGY,
2004,
11
(03)
: 146
-
150
[9]
The Chapel Hill hemophilia A dog colony exhibits a factor VIII gene inversion
Lozier, JN
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Lozier, JN
Dutra, A
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Dutra, A
Pak, E
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Pak, E
Zhou, N
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Zhou, N
Zheng, ZL
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Zheng, ZL
Nichols, TC
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Nichols, TC
Bellinger, DA
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Bellinger, DA
Read, M
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Read, M
Morgan, RA
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Morgan, RA
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2002,
99
(20)
: 12991
-
12996
[10]
Helper-dependent adenoviral gene therapy mediates long-term correction of the clotting defect in the canine hemophilia A model
McCormack, W. M.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
McCormack, W. M.
Seiler, M. P.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Seiler, M. P.
Bertin, T. K.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Bertin, T. K.
Ubhayakar, K.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Ubhayakar, K.
Palmer, D. J. .
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Palmer, D. J. .
Ng, P.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Ng, P.
Nichols, T. C.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Nichols, T. C.
Lee, B.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Lee, B.
[J].
JOURNAL OF THROMBOSIS AND HAEMOSTASIS,
2006,
4
(06)
: 1218
-
1225
←
1
2
→
共 16 条
[1]
FACTOR-VIII GENE INVERSIONS IN SEVERE HEMOPHILIA-A - RESULTS OF AN INTERNATIONAL CONSORTIUM STUDY
ANTONARAKIS, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
ANTONARAKIS, SE
ROSSITER, JP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
ROSSITER, JP
YOUNG, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
YOUNG, M
HORST, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
HORST, J
DEMOERLOOSE, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
DEMOERLOOSE, P
SOMMER, SS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SOMMER, SS
KETTERLING, RP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KETTERLING, RP
KAZAZIAN, HH
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KAZAZIAN, HH
NEGRIER, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
NEGRIER, C
VINCIGUERRA, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VINCIGUERRA, C
GITSCHIER, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GITSCHIER, J
GOOSSENS, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GOOSSENS, M
GIRODON, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GIRODON, E
GHANEM, N
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GHANEM, N
PLASSA, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PLASSA, F
LAVERGNE, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LAVERGNE, JM
VIDAUD, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VIDAUD, M
COSTA, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
COSTA, JM
LAURIAN, Y
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LAURIAN, Y
LIN, SW
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LIN, SW
LIN, SR
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LIN, SR
SHEN, MC
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SHEN, MC
LILLICRAP, D
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LILLICRAP, D
TAYLOR, SAM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
TAYLOR, SAM
WINDSOR, S
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
WINDSOR, S
VALLEIX, SV
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VALLEIX, SV
NAFA, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
NAFA, K
SULTAN, Y
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SULTAN, Y
DELPECH, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
DELPECH, M
VNENCAKJONES, CL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
VNENCAKJONES, CL
PHILLIPS, JA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PHILLIPS, JA
LJUNG, RCR
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
LJUNG, RCR
KOUMBARELIS, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KOUMBARELIS, E
GIALERAKI, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GIALERAKI, A
MANDALAKI, T
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
MANDALAKI, T
JENKINS, PV
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
JENKINS, PV
COLLINS, PW
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
COLLINS, PW
PASI, KJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PASI, KJ
GOODEVE, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GOODEVE, A
PEAKE, I
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PEAKE, I
PRESTON, FE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
PRESTON, FE
SCHWARTZ, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SCHWARTZ, M
SCHEIBEL, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
SCHEIBEL, E
INGERSLEV, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
INGERSLEV, J
COOPER, DN
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
COOPER, DN
MILLAR, DS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
MILLAR, DS
KAKKAR, VV
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
KAKKAR, VV
GIANNELLI, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
GIANNELLI, F
NAYLOR, JA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
NAYLOR, JA
TIZZANO, EF
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV GENEVA, SCH MED, CH-1211 GENEVA, SWITZERLAND
TIZZANO, EF
[J].
BLOOD,
1995,
86
(06)
: 2206
-
2212
[2]
Helper-dependent adenoviral vectors mediate therapeutic factor VIII expression for several months with minimal accompanying toxicity in a canine model of severe hemophilia A
Brown, BD
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Brown, BD
Shi, CX
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Shi, CX
Powell, S
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Powell, S
Hurlbut, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Hurlbut, D
Graham, FL
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Graham, FL
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Queens Univ, Dept Pathol & Mol Med, Richardson Lab, Kingston, ON K7L 3N6, Canada
Lillicrap, D
[J].
BLOOD,
2004,
103
(03)
: 804
-
810
[3]
Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors
Chuah, MKL
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Chuah, MKL
Schiedner, G
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Schiedner, G
Thorrez, L
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Thorrez, L
Brown, B
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Brown, B
Johnston, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Johnston, M
Gillijns, V
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Gillijns, V
Hertel, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Hertel, S
Van Rooijen, N
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Van Rooijen, N
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Lillicrap, D
Collen, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Collen, D
VandenDriessche, T
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
VandenDriessche, T
Kochanek, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, B-3000 Leuven, Belgium
Kochanek, S
[J].
BLOOD,
2003,
101
(05)
: 1734
-
1743
[4]
A gene-deleted adenoviral vector results in phenotypic correction of canine hemophilia B without liver toxicity or thrombocytopenia
Ehrhardt, A
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Ehrhardt, A
Xu, H
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Xu, H
Dillow, AM
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Dillow, AM
Bellinger, DA
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Bellinger, DA
Nichols, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Nichols, TC
Kay, MA
论文数:
0
引用数:
0
h-index:
0
机构:
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Stanford Univ, Sch Med, Dept Pediat, Stanford, CA 94305 USA
Kay, MA
[J].
BLOOD,
2003,
102
(07)
: 2403
-
2411
[5]
Germline alteration by gene therapy: assessing and reducing the risks
Gordon, JW
论文数:
0
引用数:
0
h-index:
0
机构:
Mt Sinai Med Ctr, Dept Neurobiol, New York, NY 10029 USA
Gordon, JW
[J].
MOLECULAR MEDICINE TODAY,
1998,
4
(11):
: 468
-
470
[6]
Gene therapy for hemophilia: an imperative to succeed
Hough, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Hough, C
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol & Mol Med, Kingston, ON K7L 3N6, Canada
Lillicrap, D
[J].
JOURNAL OF THROMBOSIS AND HAEMOSTASIS,
2005,
3
(06)
: 1195
-
1205
[7]
Aberrant splicing and premature termination of transcription of the FVIII gene as a cause of severe canine hemophilia A: Similarities with the intron 22 inversion mutation in human hemophilia
Hough, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Hough, C
Kamisue, S
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Kamisue, S
Cameron, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Cameron, C
Notley, C
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Notley, C
Tinlin, S
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Tinlin, S
Giles, A
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Giles, A
Lillicrap, D
论文数:
0
引用数:
0
h-index:
0
机构:
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Queens Univ, Richardson Lab, Dept Pathol, Kingston, ON K7L 3N6, Canada
Lillicrap, D
[J].
THROMBOSIS AND HAEMOSTASIS,
2002,
87
(04)
: 659
-
665
[8]
Factor VIII alloantibodies in hemophilia
Jacquemin, MG
论文数:
0
引用数:
0
h-index:
0
机构:
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Jacquemin, MG
Saint-Remy, JMR
论文数:
0
引用数:
0
h-index:
0
机构:
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Katholieke Univ Leuven, Ctr Mol & Vasc Biol, B-3000 Louvain, Belgium
Saint-Remy, JMR
[J].
CURRENT OPINION IN HEMATOLOGY,
2004,
11
(03)
: 146
-
150
[9]
The Chapel Hill hemophilia A dog colony exhibits a factor VIII gene inversion
Lozier, JN
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Lozier, JN
Dutra, A
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Dutra, A
Pak, E
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Pak, E
Zhou, N
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Zhou, N
Zheng, ZL
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Zheng, ZL
Nichols, TC
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Nichols, TC
Bellinger, DA
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Bellinger, DA
Read, M
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Read, M
Morgan, RA
论文数:
0
引用数:
0
h-index:
0
机构:
US FDA, Ctr Biol Evaluat & Res, Rockville, MD 20852 USA
Morgan, RA
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2002,
99
(20)
: 12991
-
12996
[10]
Helper-dependent adenoviral gene therapy mediates long-term correction of the clotting defect in the canine hemophilia A model
McCormack, W. M.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
McCormack, W. M.
Seiler, M. P.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Seiler, M. P.
Bertin, T. K.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Bertin, T. K.
Ubhayakar, K.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Ubhayakar, K.
Palmer, D. J. .
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Palmer, D. J. .
Ng, P.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Ng, P.
Nichols, T. C.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Nichols, T. C.
Lee, B.
论文数:
0
引用数:
0
h-index:
0
机构:
Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
Lee, B.
[J].
JOURNAL OF THROMBOSIS AND HAEMOSTASIS,
2006,
4
(06)
: 1218
-
1225
←
1
2
→