Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement

被引：148

作者：

Aiuti, A

Vai, S

Mortellaro, A

Casorati, G

Ficara, F

Andolfi, G

Ferrari, G

Tabucchi, A

Carlucci, F

Ochs, HD

Notarangelo, LD

Roncarolo, MG

Bordignon, C ^{[1
]}

机构：

[1] San Raffaele Telethon Inst Gene Therapy, HSR TIGET, Milan, Italy

[2] Sci Inst HS Raffaele, Canc Immunotherapy & Gene Therapy Program, Milan, Italy

[3] Univ Siena, Ist Biochim & Enzimol, I-53100 Siena, Italy

[4] Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA

[5] Univ Vita Salute San Raffaele, Milan, Italy

[6] Clin Pediat Brescia, Brescia, Italy

来源：

NATURE MEDICINE | 2002年 / 8卷 / 05期

关键词：

D O I：

10.1038/nm0502-423

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

引用

页码：423 / 425

页数：3

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