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Round two for liver gene therapy
被引:21
作者
:
Wilson, JM
论文数:
0
引用数:
0
h-index:
0
Wilson, JM
机构
:
来源
:
NATURE GENETICS
|
1996年
/ 12卷
/ 03期
关键词
:
D O I
:
10.1038/ng0396-232
中图分类号
:
Q3 [遗传学];
学科分类号
:
071007 ;
090102 ;
摘要
:
引用
收藏
页码:232 / 233
页数:2
相关论文
共 10 条
[1]
CHOWDHURY JR, 1991, SCIENCE, V254, P1802, DOI 10.1126/science.1722351
[2]
LOSS OF FUMARYLACETOACETATE HYDROLASE IS RESPONSIBLE FOR THE NEONATAL HEPATIC-DYSFUNCTION PHENOTYPE OF LETHAL ALBINO MICE
[J].
论文数:
引用数:
h-index:
机构:
GROMPE, M
;
ALDHALIMY, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
ALDHALIMY, M
;
FINEGOLD, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
FINEGOLD, M
;
OU, CN
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
OU, CN
;
BURLINGAME, T
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
BURLINGAME, T
;
KENNAWAY, NG
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
KENNAWAY, NG
;
SORIANO, P
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
SORIANO, P
.
GENES & DEVELOPMENT,
1993,
7
(12A)
:2298
-2307
[3]
PHARMACOLOGICAL CORRECTION OF NEONATAL LETHAL HEPATIC-DYSFUNCTION IN A MURINE MODEL OF HEREDITARY TYROSINEMIA TYPE-I
[J].
论文数:
引用数:
h-index:
机构:
GROMPE, M
;
LINDSTEDT, S
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
LINDSTEDT, S
;
ALDHALIMY, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
ALDHALIMY, M
;
KENNAWAY, NG
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
KENNAWAY, NG
;
PAPACONSTANTINOU, J
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
PAPACONSTANTINOU, J
;
TORRESRAMOS, CA
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
TORRESRAMOS, CA
;
OU, CN
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
OU, CN
;
FINEGOLD, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
FINEGOLD, M
.
NATURE GENETICS,
1995,
10
(04)
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-460
[4]
A PILOT-STUDY OF EX-VIVO GENE-THERAPY FOR HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
[J].
GROSSMAN, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
GROSSMAN, M
;
RADER, DJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
RADER, DJ
;
MULLER, DWM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
MULLER, DWM
;
KOLANSKY, DM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
KOLANSKY, DM
;
KOZARSKY, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
KOZARSKY, K
;
CLARK, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
CLARK, BJ
;
STEIN, EA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
STEIN, EA
;
LUPIEN, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
LUPIEN, PJ
;
BREWER, HB
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
BREWER, HB
;
RAPER, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
RAPER, SE
;
WILSON, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
WILSON, JM
.
NATURE MEDICINE,
1995,
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-1154
[5]
SUCCESSFUL EX-VIVO GENE-THERAPY DIRECTED TO LIVER IN A PATIENT WITH FAMILIAL HYPERCHOLESTEROLEMIA
[J].
GROSSMAN, M
论文数:
0
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0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
GROSSMAN, M
;
RAPER, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
RAPER, SE
;
KOZARSKY, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
KOZARSKY, K
;
STEIN, EA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
STEIN, EA
;
ENGELHARDT, JF
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
ENGELHARDT, JF
;
MULLER, D
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0
引用数:
0
h-index:
0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
MULLER, D
;
LUPIEN, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
LUPIEN, PJ
;
WILSON, JM
论文数:
0
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0
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0
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UNIV MICHIGAN,MED CTR,DEPT INTERNAL MED,ANN ARBOR,MI 48109
WILSON, JM
.
NATURE GENETICS,
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SELF-INDUCED CORRECTION OF THE GENETIC-DEFECT IN TYROSINEMIA TYPE-I
[J].
KVITTINGEN, EA
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0
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0
机构:
WILHELMINA KINDERZIKENHUIS,METAB DIS LAB,UTRECHT,NETHERLANDS
KVITTINGEN, EA
;
ROOTWELT, H
论文数:
0
引用数:
0
h-index:
0
机构:
WILHELMINA KINDERZIKENHUIS,METAB DIS LAB,UTRECHT,NETHERLANDS
ROOTWELT, H
;
BERGER, R
论文数:
0
引用数:
0
h-index:
0
机构:
WILHELMINA KINDERZIKENHUIS,METAB DIS LAB,UTRECHT,NETHERLANDS
BERGER, R
;
BRANDTZAEG, P
论文数:
0
引用数:
0
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0
机构:
WILHELMINA KINDERZIKENHUIS,METAB DIS LAB,UTRECHT,NETHERLANDS
BRANDTZAEG, P
.
JOURNAL OF CLINICAL INVESTIGATION,
1994,
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HEREDITARY TYROSINEMIA TYPE-I - SELF-INDUCED CORRECTION OF THE FUMARYLACETOACETASE DEFECT
[J].
KVITTINGEN, EA
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0
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0
h-index:
0
机构:
UNIV OSLO, RIKSHOSP, INST PATHOL, OSLO, NORWAY
KVITTINGEN, EA
;
ROOTWELT, H
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OSLO, RIKSHOSP, INST PATHOL, OSLO, NORWAY
ROOTWELT, H
;
BRANDTZAEG, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OSLO, RIKSHOSP, INST PATHOL, OSLO, NORWAY
BRANDTZAEG, P
;
BERGAN, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OSLO, RIKSHOSP, INST PATHOL, OSLO, NORWAY
BERGAN, A
;
BERGER, R
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OSLO, RIKSHOSP, INST PATHOL, OSLO, NORWAY
BERGER, R
.
JOURNAL OF CLINICAL INVESTIGATION,
1993,
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Hepatocytes corrected by gene therapy are selected in vivo in a murine model of hereditary tyrosinaemia type I
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Overturf, K
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引用数:
0
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0
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OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
Overturf, K
;
AlDhalimy, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
AlDhalimy, M
;
Tanguay, R
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
Tanguay, R
;
Brantly, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
Brantly, M
;
Ou, CN
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
Ou, CN
;
Finegold, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
Finegold, M
;
Grompe, M
论文数:
0
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0
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0
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OREGON HLTH SCI UNIV, DEPT MOLEC & MED GENET, PORTLAND, OR 97201 USA
Grompe, M
.
NATURE GENETICS,
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RHIM, JA
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0
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UNIV PENN,SCH VET MED,DEPT ANIM BIOL,PHILADELPHIA,PA 19104
RHIM, JA
;
SANDGREN, EP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,SCH VET MED,DEPT ANIM BIOL,PHILADELPHIA,PA 19104
SANDGREN, EP
;
DEGEN, JL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,SCH VET MED,DEPT ANIM BIOL,PHILADELPHIA,PA 19104
DEGEN, JL
;
PALMITER, RD
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,SCH VET MED,DEPT ANIM BIOL,PHILADELPHIA,PA 19104
PALMITER, RD
;
BRINSTER, RL
论文数:
0
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0
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0
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UNIV PENN,SCH VET MED,DEPT ANIM BIOL,PHILADELPHIA,PA 19104
BRINSTER, RL
.
SCIENCE,
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[J].
SANDGREN, EP
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0
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0
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UNIV WASHINGTON,HOWARD HUGHES MED INST,SEATTLE,WA 98195
SANDGREN, EP
;
PALMITER, RD
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,HOWARD HUGHES MED INST,SEATTLE,WA 98195
PALMITER, RD
;
HECKEL, JL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,HOWARD HUGHES MED INST,SEATTLE,WA 98195
HECKEL, JL
;
DAUGHERTY, CC
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,HOWARD HUGHES MED INST,SEATTLE,WA 98195
DAUGHERTY, CC
;
BRINSTER, RL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,HOWARD HUGHES MED INST,SEATTLE,WA 98195
BRINSTER, RL
;
DEGEN, JL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,HOWARD HUGHES MED INST,SEATTLE,WA 98195
DEGEN, JL
.
CELL,
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←
1
→
共 10 条
[1]
CHOWDHURY JR, 1991, SCIENCE, V254, P1802, DOI 10.1126/science.1722351
[2]
LOSS OF FUMARYLACETOACETATE HYDROLASE IS RESPONSIBLE FOR THE NEONATAL HEPATIC-DYSFUNCTION PHENOTYPE OF LETHAL ALBINO MICE
[J].
论文数:
引用数:
h-index:
机构:
GROMPE, M
;
ALDHALIMY, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
ALDHALIMY, M
;
FINEGOLD, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
FINEGOLD, M
;
OU, CN
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
OU, CN
;
BURLINGAME, T
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
BURLINGAME, T
;
KENNAWAY, NG
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
KENNAWAY, NG
;
SORIANO, P
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV, DEPT PEDIAT, PORTLAND, OR 97201 USA
SORIANO, P
.
GENES & DEVELOPMENT,
1993,
7
(12A)
:2298
-2307
[3]
PHARMACOLOGICAL CORRECTION OF NEONATAL LETHAL HEPATIC-DYSFUNCTION IN A MURINE MODEL OF HEREDITARY TYROSINEMIA TYPE-I
[J].
论文数:
引用数:
h-index:
机构:
GROMPE, M
;
LINDSTEDT, S
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
LINDSTEDT, S
;
ALDHALIMY, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
ALDHALIMY, M
;
KENNAWAY, NG
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
KENNAWAY, NG
;
PAPACONSTANTINOU, J
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
PAPACONSTANTINOU, J
;
TORRESRAMOS, CA
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
TORRESRAMOS, CA
;
OU, CN
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
OU, CN
;
FINEGOLD, M
论文数:
0
引用数:
0
h-index:
0
机构:
OREGON HLTH SCI UNIV,DEPT PEDIAT,PORTLAND,OR 97201
FINEGOLD, M
.
NATURE GENETICS,
1995,
10
(04)
:453
-460
[4]
A PILOT-STUDY OF EX-VIVO GENE-THERAPY FOR HOMOZYGOUS FAMILIAL HYPERCHOLESTEROLEMIA
[J].
GROSSMAN, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
GROSSMAN, M
;
RADER, DJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
RADER, DJ
;
MULLER, DWM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
MULLER, DWM
;
KOLANSKY, DM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
KOLANSKY, DM
;
KOZARSKY, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
KOZARSKY, K
;
CLARK, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
CLARK, BJ
;
STEIN, EA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
STEIN, EA
;
LUPIEN, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
LUPIEN, PJ
;
BREWER, HB
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
BREWER, HB
;
RAPER, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
RAPER, SE
;
WILSON, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN,MED CTR,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
WILSON, JM
.
NATURE MEDICINE,
1995,
1
(11)
:1148
-1154
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