Brain-directed gene therapy for lysosomal storage disease: Going well beyond the blood-brain barrier

被引：38

作者：

Sly, WS

Vogler, C

机构：

[1] St Louis Univ, Sch Med, Edward A Doisy Dept Biochem & Mol Biol, St Louis, MO 63104 USA

[2] St Louis Univ, Sch Med, Dept Pathol, St Louis, MO 63104 USA

来源：

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA | 2002年 / 99卷 / 09期

关键词：

D O I：

10.1073/pnas.102175599

中图分类号：

O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];

学科分类号：

07 ; 0710 ; 09 ;

摘要：

引用

页码：5760 / 5762

页数：3

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