Utrophin muscles in on the action

被引:15
作者
Karpati, G [1 ]
机构
[1] MCGILL UNIV,MONTREAL NEUROL INST,GENE THERAPY UNIT,MONTREAL,PQ H3A 2B4,CANADA
关键词
D O I
10.1038/nm0197-22
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
Overexpressing utrophin in muscles may prove a promising strategy for treating Duchenne muscular dystrophy but many questions remain unanswered.
引用
收藏
页码:22 / 23
页数:2
相关论文
共 18 条
[1]   Utrophin: A structural and functional comparison to dystrophin [J].
Blake, DJ ;
Tinsley, JM ;
Davies, KE .
BRAIN PATHOLOGY, 1996, 6 (01) :37-47
[2]  
Clemens PR, 1996, GENE THER, V3, P965
[3]   OVEREXPRESSION OF DYSTROPHIN IN TRANSGENIC MDX MICE ELIMINATES DYSTROPHIC SYMPTOMS WITHOUT TOXICITY [J].
COX, GA ;
COLE, NM ;
MATSUMURA, K ;
PHELPS, SF ;
HAUSCHKA, SD ;
CAMPBELL, KP ;
FAULKNER, JA ;
CHAMBERLAIN, JS .
NATURE, 1993, 364 (6439) :725-729
[4]  
DUNNEN J, 1989, AM J HUM GENET, V45, P835
[5]   DYSTROPHIN - THE PROTEIN PRODUCT OF THE DUCHENNE MUSCULAR-DYSTROPHY LOCUS [J].
HOFFMAN, EP ;
BROWN, RH ;
KUNKEL, LM .
CELL, 1987, 51 (06) :919-928
[6]   THE POTENTIAL FOR GENE-THERAPY IN DUCHENNE MUSCULAR-DYSTROPHY AND OTHER GENETIC MUSCLE DISEASES [J].
KARPATI, G ;
ACSADI, G .
MUSCLE & NERVE, 1993, 16 (11) :1141-1153
[7]   LOCALIZATION AND QUANTITATION OF THE CHROMOSOME 6-ENCODED DYSTROPHIN-RELATED PROTEIN IN NORMAL AND PATHOLOGICAL HUMAN MUSCLE [J].
KARPATI, G ;
CARPENTER, S ;
MORRIS, GE ;
DAVIES, KE ;
GUERIN, C ;
HOLLAND, P .
JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY, 1993, 52 (02) :119-128
[8]   MYOBLAST TRANSFER IN DUCHENNE MUSCULAR-DYSTROPHY [J].
KARPATI, G ;
AJDUKOVIC, D ;
ARNOLD, D ;
GLEDHILL, RB ;
GUTTMANN, R ;
HOLLAND, P ;
KOCH, PA ;
SHOUBRIDGE, E ;
SPENCE, D ;
VANASSE, M ;
WATTERS, GV ;
ABRAHAMOWICZ, M ;
DUFF, C ;
WORTON, RG .
ANNALS OF NEUROLOGY, 1993, 34 (01) :8-17
[9]  
KARPATI G, 1992, CURR OPIN NEUROL NEU, V5, P615
[10]  
KOENIG M, 1989, AM J HUM GENET, V45, P498