Treatment of idiopathic hyperphosphatasia with intensive bisphosphonate therapy

被引：41

作者：

Cundy, T

Wheadon, L

King, A

机构：

[1] Auckland Hosp, Dept Med, Fac Med & Hlth Sci, Auckland, New Zealand

[2] Kelston Deaf Educ Ctr, Auckland, New Zealand

[3] Middlemore Hosp, Dept Pathol, Auckland 6, New Zealand

来源：

JOURNAL OF BONE AND MINERAL RESEARCH | 2004年 / 19卷 / 05期

关键词：

idiopathic hyperphosphatasia; juvenile Paget's disease; bisphosphonates; children;

D O I：

10.1359/JBMR.040127

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

In a family with IH, a rare high turnover bone disease, two older siblings were wheelchair-bound with severe skeletal deformity by age 15. Their youngest affected sibling was treated intensively with intravenous bisphosphonates for 3 years. The treatment was well tolerated and prevented the development of deformity and disability.

引用

页码：703 / 711

页数：9

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