Gene Therapy Fulfilling Its Promise.

被引：74

作者：

Kohn, Donald B. ^{[1
,2
]}

Candotti, Fabio ^{[3
]}

机构：

[1] Childrens Hosp Los Angeles, Div Res Immunol Bone Marrow Transplantat, Los Angeles, CA 90027 USA

[2] Univ So Calif, Keck Sch Med, Dept Pediat, Los Angeles, CA 90033 USA

[3] NHGRI, Disorders Immun Sect, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA

来源：

NEW ENGLAND JOURNAL OF MEDICINE | 2009年 / 360卷 / 05期

关键词：

SEVERE COMBINED IMMUNODEFICIENCY; BONE-MARROW; TRANSPLANTATION; CELLS;

D O I：

10.1056/NEJMe0809614

中图分类号：

R5 [内科学];

学科分类号：

100201 [内科学];

摘要：

引用

页码：518 / 521

页数：4

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