Retinal Gene Therapy Coming of Age

被引：33

作者：

Cepko, Connie L. ^{[1
,2
,3
]}

Vandenberghe, Luk H. ^{[4
]}

机构：

[1] Harvard Univ, Sch Med, Dept Genet, Boston, MA 02114 USA

[2] Harvard Univ, Sch Med, Dept Ophthalmol, Boston, MA 02114 USA

[3] Howard Hughes Med Inst, Boston, MA 02114 USA

[4] Harvard Univ, Sch Med, Dept Ophthalmol, Schepens Eye Res Inst,Massachusetts Eye & Ear Inf, Boston, MA 02114 USA

来源：

HUMAN GENE THERAPY | 2013年 / 24卷 / 03期

关键词：

LEBER CONGENITAL AMAUROSIS; PHOTORECEPTOR DEGENERATION; VISION;

D O I：

10.1089/hum.2013.050

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：242 / 244

页数：3

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