Treatment with amino acids in serine deficiency disorders

被引:50
作者
de Koning, TJ [1 ]
机构
[1] Univ Utrecht, Med Ctr, Dept Metab Dis, NL-3508 AB Utrecht, Netherlands
关键词
D O I
10.1007/s10545-006-0269-0
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
Serine deficiency disorders are rare defects in the biosynthesis of the amino acid L-serine. At present two disorders have been reported: 3-phosphoglycerate dehydrogenase deficiency and 3-phosphoserine phosphatase deficiency. These enzyme defects lead to severe neurological symptoms such as congenital microcephaly and severe psychomotor retardation and in addition in patients with 3-phosphoglycerate dehydrogenase deficiency to intractable seizures. These symptoms respond to a variable degree to treatment with L-serine, sometimes combined with glycine. In this paper the current practice of amino acid treatment with L-serine and glycine in serine deficiency is reviewed.
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收藏
页码:347 / 351
页数:5
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