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Gene therapy: Progress, problems, prospects.
被引:31
作者
:
Blau, H
论文数:
0
引用数:
0
h-index:
0
机构:
STANFORD UNIV,SCH MED,DEPT DERMATOL,STANFORD,CA 94305
Blau, H
Khavari, P
论文数:
0
引用数:
0
h-index:
0
机构:
STANFORD UNIV,SCH MED,DEPT DERMATOL,STANFORD,CA 94305
Khavari, P
机构
:
[1]
STANFORD UNIV,SCH MED,DEPT DERMATOL,STANFORD,CA 94305
[2]
VET AFFAIRS PALO ALTO,STANFORD,CA 94305
来源
:
NATURE MEDICINE
|
1997年
/ 3卷
/ 06期
关键词
:
D O I
:
10.1038/nm0697-612
中图分类号
:
Q5 [生物化学];
Q7 [分子生物学];
学科分类号
:
071010 ;
081704 ;
摘要
:
A recent meeting highlights the progress and the challenges of gene therapy.
引用
收藏
页码:612 / 613
页数:2
相关论文
共 8 条
[1]
BOHL D, 1997, NAT MED, V3, P229
[2]
Complexes of adenovirus with polycationic polymers and cationic lipids increase the efficiency of gene transfer in vitro and in vivo
[J].
Fasbender, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Fasbender, A
;
论文数:
引用数:
h-index:
机构:
Zabner, J
;
Chillon, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Chillon, M
;
Moninger, TO
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Moninger, TO
;
Puga, AP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Puga, AP
;
Davidson, BL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Davidson, BL
;
Welsh, MJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Welsh, MJ
.
JOURNAL OF BIOLOGICAL CHEMISTRY,
1997,
272
(10)
:6479
-6489
[3]
Recombinant adeno-associated virus for muscle directed gene therapy
[J].
Fisher, KJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Fisher, KJ
;
Jooss, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Jooss, K
;
Alston, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Alston, J
;
Yang, YP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Yang, YP
;
Haecker, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Haecker, SE
;
High, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
High, K
;
Pathak, R
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Pathak, R
;
Raper, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Raper, SE
;
Wilson, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Wilson, JM
.
NATURE MEDICINE,
1997,
3
(03)
:306
-312
[4]
Insertion of the adenoviral E3 region into a recombinant viral vector prevents antiviral humoral and cellular immune responses and permits long-term gene expression
[J].
Ilan, Y
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Ilan, Y
;
Droguett, G
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Droguett, G
;
Chowdhury, NR
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Chowdhury, NR
;
Li, YA
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Li, YA
;
Sengupta, K
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Sengupta, K
;
Thummala, NR
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Thummala, NR
;
Davidson, A
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Davidson, A
;
Chowdhury, JR
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Chowdhury, JR
;
Horwitz, MS
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Horwitz, MS
.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1997,
94
(06)
:2587
-2592
[5]
LONG-TERM HEPATIC ADENOVIRUS-MEDIATED GENE-EXPRESSION IN MICE FOLLOWING CTLA4LG ADMINISTRATION
[J].
KAY, MA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
KAY, MA
;
HOLTERMAN, AX
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
HOLTERMAN, AX
;
MEUSE, L
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
MEUSE, L
;
GOWN, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
GOWN, A
;
OCHS, HD
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
OCHS, HD
;
LINSLEY, PS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
LINSLEY, PS
;
WILSON, CB
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0
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0
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0
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UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
WILSON, CB
.
NATURE GENETICS,
1995,
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Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors
[J].
Koeberl, DD
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0
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0
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FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Koeberl, DD
;
Alexander, IE
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0
引用数:
0
h-index:
0
机构:
FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Alexander, IE
;
Halbert, CL
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0
引用数:
0
h-index:
0
机构:
FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Halbert, CL
;
Russell, DW
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0
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0
h-index:
0
机构:
FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Russell, DW
;
Miller, AD
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FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Miller, AD
.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
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Efficient transfer, integration, and sustained long-term expression of the transgene in adult rat brains injected with a lentiviral vector
[J].
Naldini, L
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SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
Naldini, L
;
Blomer, U
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0
引用数:
0
h-index:
0
机构:
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
Blomer, U
;
Gage, FH
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0
引用数:
0
h-index:
0
机构:
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
Gage, FH
;
Trono, D
论文数:
0
引用数:
0
h-index:
0
机构:
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
Trono, D
;
Verma, IM
论文数:
0
引用数:
0
h-index:
0
机构:
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
SALK INST BIOL STUDIES,SAN DIEGO,CA 92186
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.
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Amelioration of the dystrophic phenotype of mdx mice using a truncated utrophin transgene
[J].
Tinsley, JM
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0
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UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
Tinsley, JM
;
Potter, AC
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0
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0
h-index:
0
机构:
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
Potter, AC
;
Phelps, SR
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
Phelps, SR
;
Fisher, R
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
Fisher, R
;
Trickett, JI
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
Trickett, JI
;
Davies, KE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
UNIV OXFORD,DEPT BIOCHEM,GENET LAB,OXFORD OX1 3QU,ENGLAND
Davies, KE
.
NATURE,
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384
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-353
←
1
→
共 8 条
[1]
BOHL D, 1997, NAT MED, V3, P229
[2]
Complexes of adenovirus with polycationic polymers and cationic lipids increase the efficiency of gene transfer in vitro and in vivo
[J].
Fasbender, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Fasbender, A
;
论文数:
引用数:
h-index:
机构:
Zabner, J
;
Chillon, M
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Chillon, M
;
Moninger, TO
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Moninger, TO
;
Puga, AP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Puga, AP
;
Davidson, BL
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Davidson, BL
;
Welsh, MJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV IOWA,COLL MED,HOWARD HUGHES MED INST,DEPT INTERNAL MED,IOWA CITY,IA 52242
Welsh, MJ
.
JOURNAL OF BIOLOGICAL CHEMISTRY,
1997,
272
(10)
:6479
-6489
[3]
Recombinant adeno-associated virus for muscle directed gene therapy
[J].
Fisher, KJ
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Fisher, KJ
;
Jooss, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Jooss, K
;
Alston, J
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Alston, J
;
Yang, YP
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Yang, YP
;
Haecker, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Haecker, SE
;
High, K
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
High, K
;
Pathak, R
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Pathak, R
;
Raper, SE
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Raper, SE
;
Wilson, JM
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV PENN HLTH SYST,INST HUMAN GENE THERAPY,PHILADELPHIA,PA 19104
Wilson, JM
.
NATURE MEDICINE,
1997,
3
(03)
:306
-312
[4]
Insertion of the adenoviral E3 region into a recombinant viral vector prevents antiviral humoral and cellular immune responses and permits long-term gene expression
[J].
Ilan, Y
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Ilan, Y
;
Droguett, G
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Droguett, G
;
Chowdhury, NR
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Chowdhury, NR
;
Li, YA
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Li, YA
;
Sengupta, K
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Sengupta, K
;
Thummala, NR
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Thummala, NR
;
Davidson, A
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Davidson, A
;
Chowdhury, JR
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Chowdhury, JR
;
Horwitz, MS
论文数:
0
引用数:
0
h-index:
0
机构:
ALBERT EINSTEIN COLL MED, DEPT MICROBIOL & IMMUNOL, BRONX, NY 10461 USA
Horwitz, MS
.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1997,
94
(06)
:2587
-2592
[5]
LONG-TERM HEPATIC ADENOVIRUS-MEDIATED GENE-EXPRESSION IN MICE FOLLOWING CTLA4LG ADMINISTRATION
[J].
KAY, MA
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
KAY, MA
;
HOLTERMAN, AX
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
HOLTERMAN, AX
;
MEUSE, L
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
MEUSE, L
;
GOWN, A
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
GOWN, A
;
OCHS, HD
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
OCHS, HD
;
LINSLEY, PS
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
LINSLEY, PS
;
WILSON, CB
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV WASHINGTON,DEPT PEDIAT,SEATTLE,WA 98195
WILSON, CB
.
NATURE GENETICS,
1995,
11
(02)
:191
-197
[6]
Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors
[J].
Koeberl, DD
论文数:
0
引用数:
0
h-index:
0
机构:
FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Koeberl, DD
;
Alexander, IE
论文数:
0
引用数:
0
h-index:
0
机构:
FRED HUTCHINSON CANC RES CTR,SEATTLE,WA 98109
Alexander, IE
;
Halbert, CL
论文数:
0
引用数:
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