Gene therapy for human SCID: Dreams become reality

被引：21

作者：

Buckley, RH ^{[1
]}

机构：

[1] Duke Univ, Med Ctr, Dept Pediat & Immunol, Durham, NC 27710 USA

来源：

NATURE MEDICINE | 2000年 / 6卷 / 06期

关键词：

D O I：

10.1038/76185

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

After a decade of unsuccessful attempts to correct one form of severe combined immunodeficiency using gene therapy, success has finally been achieved in another genetic type. Whether this success is due to the type of defect or to other factors, such as improved retroviral vectors or stem cell growth conditions, is not yet apparent.

引用

页码：623 / 624

页数：2

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