共 5 条
[1]
Bhide PG, 1996, J NEUROSCI, V16, P5523
[2]
Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis
[J].
Kordasiewicz, Holly B.
;
Stanek, Lisa M.
;
Wancewicz, Edward V.
;
Mazur, Curt
;
McAlonis, Melissa M.
;
Pytel, Kimberly A.
;
Artates, Jonathan W.
;
Weiss, Andreas
;
Cheng, Seng H.
;
Shihabuddin, Lamya S.
;
Hung, Gene
;
Bennett, C. Frank
;
Cleveland, Don W.
.
NEURON,
2012, 74 (06)
:1031-1044

Kordasiewicz, Holly B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA
Univ Calif San Diego, Dept Cellular & Mol Med, La Jolla, CA 92093 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Stanek, Lisa M.
论文数: 0 引用数: 0
h-index: 0
机构:
Genzyme Corp, Framingham, MA 01760 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Wancewicz, Edward V.
论文数: 0 引用数: 0
h-index: 0
机构:
Isis Pharmaceut, Carlsbad, CA 92010 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Mazur, Curt
论文数: 0 引用数: 0
h-index: 0
机构:
Isis Pharmaceut, Carlsbad, CA 92010 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

McAlonis, Melissa M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA
Univ Calif San Diego, Dept Cellular & Mol Med, La Jolla, CA 92093 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Pytel, Kimberly A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA
Univ Calif San Diego, Dept Cellular & Mol Med, La Jolla, CA 92093 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Artates, Jonathan W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA
Univ Calif San Diego, Dept Cellular & Mol Med, La Jolla, CA 92093 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Weiss, Andreas
论文数: 0 引用数: 0
h-index: 0
机构:
Novartis Inst BioMed Res, CH-4002 Basel, Switzerland Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Cheng, Seng H.
论文数: 0 引用数: 0
h-index: 0
机构:
Genzyme Corp, Framingham, MA 01760 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Shihabuddin, Lamya S.
论文数: 0 引用数: 0
h-index: 0
机构:
Genzyme Corp, Framingham, MA 01760 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Hung, Gene
论文数: 0 引用数: 0
h-index: 0
机构:
Isis Pharmaceut, Carlsbad, CA 92010 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Bennett, C. Frank
论文数: 0 引用数: 0
h-index: 0
机构:
Isis Pharmaceut, Carlsbad, CA 92010 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA

Cleveland, Don W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA
Univ Calif San Diego, Dept Cellular & Mol Med, La Jolla, CA 92093 USA Univ Calif San Diego, Ludwig Inst Canc Res, La Jolla, CA 92093 USA
[3]
"Huntingtin Holiday": Progress toward an Antisense Therapy for Huntington's Disease
[J].
Lu, Xiao-Hong
;
Yang, X. William
.
NEURON,
2012, 74 (06)
:964-966

Lu, Xiao-Hong
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Ctr Neurobehav Genet, Semel Inst Neurosci & Human Behav, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Psychiat & Biobehav Sci, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Inst Brain Res, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Ctr Neurobehav Genet, Semel Inst Neurosci & Human Behav, Los Angeles, CA 90095 USA

Yang, X. William
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Ctr Neurobehav Genet, Semel Inst Neurosci & Human Behav, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Dept Psychiat & Biobehav Sci, Los Angeles, CA 90095 USA
Univ Calif Los Angeles, David Geffen Sch Med, Inst Brain Res, Los Angeles, CA 90095 USA Univ Calif Los Angeles, David Geffen Sch Med, Ctr Neurobehav Genet, Semel Inst Neurosci & Human Behav, Los Angeles, CA 90095 USA
[4]
Oligonucleotide therapeutic approaches for Huntington disease
[J].
Sah, Dinah W. Y.
;
Aronin, Neil
.
JOURNAL OF CLINICAL INVESTIGATION,
2011, 121 (02)
:500-507

Sah, Dinah W. Y.
论文数: 0 引用数: 0
h-index: 0
机构:
Alnylam Pharmaceut Inc, Cambridge, MA USA Univ Massachusetts, Sch Med, Worcester, MA 01655 USA

Aronin, Neil
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Massachusetts, Sch Med, Worcester, MA 01655 USA Univ Massachusetts, Sch Med, Worcester, MA 01655 USA
[5]
HOMOZYGOTES FOR HUNTINGTONS-DISEASE
[J].
WEXLER, NS
;
YOUNG, AB
;
TANZI, RE
;
TRAVERS, H
;
STAROSTARUBINSTEIN, S
;
PENNEY, JB
;
SNODGRASS, SR
;
SHOULSON, I
;
GOMEZ, F
;
ARROYO, MAR
;
PENCHASZADEH, GK
;
MORENO, H
;
GIBBONS, K
;
FARYNIARZ, A
;
HOBBS, W
;
ANDERSON, MA
;
BONILLA, E
;
CONNEALLY, PM
;
GUSELLA, JF
.
NATURE,
1987, 326 (6109)
:194-197

WEXLER, NS
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

YOUNG, AB
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

TANZI, RE
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

TRAVERS, H
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

STAROSTARUBINSTEIN, S
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

PENNEY, JB
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

SNODGRASS, SR
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

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GOMEZ, F
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

ARROYO, MAR
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

PENCHASZADEH, GK
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

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GIBBONS, K
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

FARYNIARZ, A
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

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BONILLA, E
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

CONNEALLY, PM
论文数: 0 引用数: 0
h-index: 0
机构: COLUMBIA UNIV COLL PHYS & SURG,DEPT NEUROL,NEW YORK,NY 10032

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