ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering

被引:2502
作者
Gaj, Thomas [1 ,2 ,3 ]
Gersbach, Charles A. [4 ,5 ]
Barbas, Carlos F., III [1 ,2 ,3 ]
机构
[1] Scripps Res Inst, Skaggs Inst Chem Biol, La Jolla, CA 92037 USA
[2] Scripps Res Inst, Dept Mol Biol, La Jolla, CA 92037 USA
[3] Scripps Res Inst, Dept Chem, La Jolla, CA 92037 USA
[4] Duke Univ, Dept Biomed Engn, Durham, NC 27706 USA
[5] Duke Univ, Inst Genome Sci & Policy, Durham, NC USA
基金
美国国家科学基金会; 美国国家卫生研究院;
关键词
zinc-finger nuclease; transcription activator-like effector nuclease; clustered regulatory interspaced short palindromic repeat; genome engineering; ZINC-FINGER NUCLEASES; TARGETED GENE DISRUPTION; DOUBLE-STRAND BREAKS; EMBRYO MICROINJECTION; KNOCKOUT RATS; HUMAN-CELLS; T-CELLS; DNA; INTEGRATION; DESIGN;
D O I
10.1016/j.tibtech.2013.04.004
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
Zinc-finger nucleases (ZFNs) and transcription activator-like effector nucleases (TALENs) comprise a powerful class of tools that are redefining the boundaries of biological research. These chimeric nucleases are composed of programmable, sequence-specific DNA-binding modules linked to a nonspecific DNA cleavage domain. ZFNs and TALENs enable a broad range of genetic modifications by inducing DNA double-strand breaks that stimulate error-prone nonhomologous end joining or homology-directed repair at specific genomic locations. Here, we review achievements made possible by site-specific nuclease technologies and discuss applications of these reagents for genetic analysis and manipulation. In addition, we highlight the therapeutic potential of ZFNs and TALENs and discuss future prospects for the field, including the emergence of clustered regulatory interspaced short palindromic repeat (CRISPR)/Cas-based RNA-guided DNA endonucleases.
引用
收藏
页码:397 / 405
页数:9
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