Intramuscular Administration of AAV1-Lipoprotein LipaseS447X Lowers Triglycerides in Lipoprotein Lipase-Deficient Patients

被引：160

作者：

Stroes, Erik S.

Nierman, Melchior C.

Meulenberg, Janneke J. ^{[6
]}

Franssen, Remco

Twisk, Jaap ^{[6
]}

Henny, C. Pieter ^{[1
]}

Maas, Mario M. ^{[2
]}

Zwinderman, Aeilko H. ^{[3
]}

Ross, Colin ^{[7
]}

Aronica, Eleonora ^{[4
]}

High, Katherine A. ^{[8
]}

Levi, Marcel M. ^{[5
]}

Hayden, Michael R. ^{[7
]}

Kastelein, John J. ^{[1
]}

Kuivenhoven, Jan Albert

机构：

[1] AMC, Dept Anaesthesiol, NL-1105 AZ Amsterdam, Netherlands

[2] AMC, Dept Radiol, NL-1105 AZ Amsterdam, Netherlands

[3] AMC, Dept Biostat, NL-1105 AZ Amsterdam, Netherlands

[4] AMC, Dept Neuropathol, NL-1105 AZ Amsterdam, Netherlands

[5] AMC, Dept Internal Med, NL-1105 AZ Amsterdam, Netherlands

[6] Amsterdam Mol Therapeut, Amsterdam, Netherlands

[7] Univ British Columbia, Ctr Mol Med & Therapeut, Vancouver, BC V5Z 1M9, Canada

[8] Univ Penn, Childrens Hosp, Sch Med, Philadelphia, PA 19104 USA

来源：

ARTERIOSCLEROSIS THROMBOSIS AND VASCULAR BIOLOGY | 2008年 / 28卷 / 12期

关键词：

D O I：

10.1161/ATVBAHA.108.175620

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

[No abstract available]

引用

页码：2303 / U264

页数：10

共 3 条

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