Congenital central hypoventilation syndrome and Hirschsprung's disease in an extremely preterm infant

被引:26
作者
Bajaj, R
Smith, J
Trochet, D
Pitkin, J
Ouvrier, R
Graf, N
Sillence, D
Kluckow, M
机构
[1] Royal N Shore Hosp, St Leonards, NSW 2065, Australia
[2] Childrens Hosp, Westmead, NSW, Australia
[3] Univ Sydney, Discipline Paediat & Child Hlth, Sydney, NSW 2006, Australia
[4] INSERM, U393, Unite Rech Handicaps Genet Enfant, Paris, France
[5] Hop Necker Enfants Malad, Dept Genet, Paris, France
关键词
aganglionosis; hypoventilation; preterm infant; congenital central hypoventilation syndrome;
D O I
10.1542/peds.2004-1910
中图分类号
R72 [儿科学];
学科分类号
100202 ;
摘要
Congenital central hypoventilation syndrome with Hirschsprung's disease, also known as Haddad syndrome, is a rare disorder with a variable phenotypic severity. The underlying cause is thought to be an abnormality of neural crest development and/or migration. Surviving neonates can have generalized autonomic nervous system dysfunction. Recent reports have identified mutations in the PHOX2B gene in a significant number of patients with this disorder. Diagnosis and management of this disorder in the setting of extreme prematurity is difficult as the manifestations of failure to maintain breathing effort and failure to establish feeds overlap with the complications of prematurity. We describe an infant who had congenital central hypoventilation syndrome with Hirschsprung's disease and was delivered at 26 weeks' gestational age and had total aganglionosis of the bowel, failure to wean from ventilation, and a mutation in the PHOX2B gene.
引用
收藏
页码:E737 / E738
页数:2
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