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Hematopoietic cell therapy for metabolic disease
被引:66
作者
:
Orchard, Paul J.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
Orchard, Paul J.
Blazar, Bruce R.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
Blazar, Bruce R.
Wagner, John
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
Wagner, John
Charnas, Lawrence
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
Charnas, Lawrence
Krivit, William
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
Krivit, William
Tolar, Jakub
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
Tolar, Jakub
机构
:
[1]
Univ Minnesota, Div Hematol Oncol, Dept Pediat, Minneapolis, MN USA
[2]
Univ Minnesota, Div Pediat Clin Neurosci, Dept Pediat, Minneapolis, MN USA
来源
:
JOURNAL OF PEDIATRICS
|
2007年
/ 151卷
/ 04期
关键词
:
D O I
:
10.1016/j.jpeds.2007.04.054
中图分类号
:
R72 [儿科学];
学科分类号
:
100202 ;
摘要
:
[No abstract available]
引用
收藏
页码:340 / 346
页数:7
相关论文
共 60 条
[1]
Human mesenchymal stem cells modulate allogeneic immune cell responses
[J].
Aggarwal, S
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0
引用数:
0
h-index:
0
机构:
Osiris Therapeut, Baltimore, MD 21231 USA
Osiris Therapeut, Baltimore, MD 21231 USA
Aggarwal, S
;
Pittenger, MF
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Osiris Therapeut, Baltimore, MD 21231 USA
Osiris Therapeut, Baltimore, MD 21231 USA
Pittenger, MF
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BLOOD,
2005,
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[2]
Enzyme replacement for lysosomal diseases
[J].
Brady, RO
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Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branc, NIH, Bethesda, MD 20892 USA
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Brady, RO
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ANNUAL REVIEW OF MEDICINE,
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:283
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[3]
Usefulness of bone marrow transplantation in the Hurler syndrome
[J].
Braunlin, EA
论文数:
0
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Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Braunlin, EA
;
Stauffer, NR
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0
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Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
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;
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;
Hopwood, JJ
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Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
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;
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论文数:
0
引用数:
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h-index:
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机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
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.
AMERICAN JOURNAL OF CARDIOLOGY,
2003,
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(07)
:882
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[4]
Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome
[J].
Cox-Brinkman, J.
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0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
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;
Boelens, J. -J.
论文数:
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引用数:
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Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
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;
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NYU, Mt Sinai Sch Med, Dept Human Genet, New York, NY 10029 USA
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[6]
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APPELMANS, F
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[7]
Gene therapy for lysosomal storage diseases: the lessons and promise of animal models
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Ellinwood, NM
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Univ Pittsburgh, Dept Pathobiol, Philadelphia, PA 19104 USA
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
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1
2
3
4
5
6
→
共 60 条
[1]
Human mesenchymal stem cells modulate allogeneic immune cell responses
[J].
Aggarwal, S
论文数:
0
引用数:
0
h-index:
0
机构:
Osiris Therapeut, Baltimore, MD 21231 USA
Osiris Therapeut, Baltimore, MD 21231 USA
Aggarwal, S
;
Pittenger, MF
论文数:
0
引用数:
0
h-index:
0
机构:
Osiris Therapeut, Baltimore, MD 21231 USA
Osiris Therapeut, Baltimore, MD 21231 USA
Pittenger, MF
.
BLOOD,
2005,
105
(04)
:1815
-1822
[2]
Enzyme replacement for lysosomal diseases
[J].
Brady, RO
论文数:
0
引用数:
0
h-index:
0
机构:
Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branc, NIH, Bethesda, MD 20892 USA
Natl Inst Neurol Disorders & Stroke, Dev & Metab Neurol Branc, NIH, Bethesda, MD 20892 USA
Brady, RO
.
ANNUAL REVIEW OF MEDICINE,
2006,
57
:283
-296
[3]
Usefulness of bone marrow transplantation in the Hurler syndrome
[J].
Braunlin, EA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Braunlin, EA
;
Stauffer, NR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Stauffer, NR
;
Peters, CH
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Peters, CH
;
Bass, JL
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Bass, JL
;
Berry, JM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Berry, JM
;
Hopwood, JJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Hopwood, JJ
;
Krivit, W
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Minnesota, Sch Med, Minneapolis, MN 55455 USA
Krivit, W
.
AMERICAN JOURNAL OF CARDIOLOGY,
2003,
92
(07)
:882
-886
[4]
Haematopoietic cell transplantation (HCT) in combination with enzyme replacement therapy (ERT) in patients with Hurler syndrome
[J].
Cox-Brinkman, J.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Cox-Brinkman, J.
;
Boelens, J. -J.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Boelens, J. -J.
;
Wraith, J. E.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Wraith, J. E.
;
O'Meara, A.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
O'Meara, A.
;
Veys, P.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Veys, P.
;
Wijburg, F. A.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Wijburg, F. A.
;
Wulffraat, N.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Wulffraat, N.
;
Wynn, R. F.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Utrecht, Med Ctr, Wilhelmina Childrens Hosp, BMT,Dept Immunol, NL-3508 AB Utrecht, Netherlands
Wynn, R. F.
.
BONE MARROW TRANSPLANTATION,
2006,
38
(01)
:17
-21
[5]
Enzyme replacement and enhancement therapies for lysosomal diseases
[J].
Desnick, RJ
论文数:
0
引用数:
0
h-index:
0
机构:
NYU, Mt Sinai Sch Med, Dept Human Genet, New York, NY 10029 USA
NYU, Mt Sinai Sch Med, Dept Human Genet, New York, NY 10029 USA
Desnick, RJ
.
JOURNAL OF INHERITED METABOLIC DISEASE,
2004,
27
(03)
:385
-410
[6]
TISSUE FRACTIONATION STUDIES .6. INTRACELLULAR DISTRIBUTION PATTERNS OF ENZYMES IN RAT-LIVER TISSUE
[J].
DUVE, CD
论文数:
0
引用数:
0
h-index:
0
DUVE, CD
;
PRESSMAN, BC
论文数:
0
引用数:
0
h-index:
0
PRESSMAN, BC
;
GIANETTO, R
论文数:
0
引用数:
0
h-index:
0
GIANETTO, R
;
WATTIAUX, R
论文数:
0
引用数:
0
h-index:
0
WATTIAUX, R
;
APPELMANS, F
论文数:
0
引用数:
0
h-index:
0
APPELMANS, F
.
BIOCHEMICAL JOURNAL,
1955,
60
(1-4)
:604
-617
[7]
Gene therapy for lysosomal storage diseases: the lessons and promise of animal models
[J].
Ellinwood, NM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Pittsburgh, Dept Pathobiol, Philadelphia, PA 19104 USA
Ellinwood, NM
;
Vite, CH
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Pittsburgh, Dept Pathobiol, Philadelphia, PA 19104 USA
Vite, CH
;
Haskins, ME
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Pittsburgh, Dept Pathobiol, Philadelphia, PA 19104 USA
Haskins, ME
.
JOURNAL OF GENE MEDICINE,
2004,
6
(05)
:481
-506
[8]
A staging system for infantile Krabbe disease to predict outcome after unrelated umbilical cord blood transplantation
[J].
Escolar, Maria L.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Escolar, Maria L.
;
Poe, Michele D.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Poe, Michele D.
;
Martin, Holly R.
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Martin, Holly R.
;
Kurtzberg, Joanne
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Kurtzberg, Joanne
.
PEDIATRICS,
2006,
118
(03)
:E879
-E889
[9]
Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease
[J].
Escolar, ML
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Escolar, ML
;
Poe, MD
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Poe, MD
;
Provenzale, JM
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Provenzale, JM
;
Richards, KC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Richards, KC
;
Allison, J
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Allison, J
;
Wood, S
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Wood, S
;
Wenger, DA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Wenger, DA
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0
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0
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Pietryga, D
;
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0
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0
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Wall, D
;
Champagne, M
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0
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0
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Champagne, M
;
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0
引用数:
0
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Morse, R
;
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0
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
Krivit, W
;
Kurtzberg, J
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Univ N Carolina, Clin Ctr Study Dev & Learning, Program Neurodev Funct Rare Disorders, Chapel Hill, NC 27599 USA
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