Workshop on shedding data from gene therapy studies with viral vectors. Amsterdam, January 22, 2004

被引：3

作者：

Bleijs, DA ^{[1
]}

机构：

[1] Netherlands Commiss Genet Modificat, NL-3720 AN Bilthoven, Netherlands

来源：

JOURNAL OF GENE MEDICINE | 2005年 / 7卷 / 02期

关键词：

gene therapy; shedding; biodistribution; viral vectors; biosafety; risk analysis;

D O I：

10.1002/jgm.689

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：256 / 259

页数：4

共 5 条

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Osborne, CS ;

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Cohen, JI ;

de Saint Basile, G ;

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Wintergerst, U ;

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Romana, S ;

Radford-Weiss, I ;

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Valensi, F ;

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[4] AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B [J].

Manno, CS ;

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Herzog, RW ;

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Ozelo, M ;

Couto, LB ;

Leonard, DGB ;

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[5] Activation of the T-cell oncogene LMO2 after gene therapy for X-linked severe combined immunodeficiency [J].

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