AAVant-garde gene therapy

被引：17

作者：

Linden, RM ^{[1
]}

Woo, SLC ^{[1
]}

机构：

[1] CUNY Mt Sinai Sch Med, Inst Gene Therapy & Mol Med, New York, NY 10029 USA

来源：

NATURE MEDICINE | 1999年 / 5卷 / 01期

关键词：

D O I：

10.1038/4698

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

Using a recombinant adeno-associated virus vector to deliver the factor IX gene, two groups achieve long-term partial correction of hemophilia B in a canine model of the disease (pages 56–70).

引用

页码：21 / 22

页数：2

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