Development of optimized vectors for gene therapy

被引:50
作者
Nabel, GJ [1 ]
机构
[1] Univ Michigan, Dept Internal Med & Biol Chem, Howard Hughes Med Inst, Ann Arbor, MI 48109 USA
关键词
D O I
10.1073/pnas.96.2.324
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页码:324 / 326
页数:3
相关论文
共 23 条
[1]   Adenovirus-mediated regulable target gene expression in vivo [J].
Burcin, MM ;
Schiedner, G ;
Kochanek, S ;
Tsai, SY ;
O'Malley, BW .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1999, 96 (02) :355-360
[2]   Role of E4 in eliciting CD4 T-cell and B-cell responses to adenovirus vectors delivered to murine and nonhuman primate lungs [J].
Chirmule, N ;
Hughes, JV ;
Gao, GP ;
Raper, SE ;
Wilson, JM .
JOURNAL OF VIROLOGY, 1998, 72 (07) :6138-6145
[3]   A 5' ELEMENT OF THE CHICKEN BETA-GLOBIN DOMAIN SERVES AS AN INSULATOR IN HUMAN ERYTHROID-CELLS AND PROTECTS AGAINST POSITION EFFECT IN DROSOPHILA [J].
CHUNG, JH ;
WHITELEY, M ;
FELSENFELD, G .
CELL, 1993, 74 (03) :505-514
[4]  
Clemens PR, 1996, GENE THER, V3, P965
[5]   CELLULAR AND HUMORAL IMMUNE-RESPONSES TO ADENOVIRAL VECTORS CONTAINING FACTOR-IX GENE - TOLERIZATION OF FACTOR-IX AND VECTOR ANTIGENS ALLOWS FOR LONG-TERM EXPRESSION [J].
DAI, YF ;
SCHWARZ, EM ;
GU, DL ;
ZHANG, WW ;
SARVETNICK, N ;
VERMA, IM .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1995, 92 (05) :1401-1405
[6]   TRANSCRIPTIONAL ACTIVATION BY TETRACYCLINES IN MAMMALIAN-CELLS [J].
GOSSEN, M ;
FREUNDLIEB, S ;
BENDER, G ;
MULLER, G ;
HILLEN, W ;
BUJARD, H .
SCIENCE, 1995, 268 (5218) :1766-1769
[7]   In vivo expression of full-length human dystrophin from adenoviral vectors deleted of all viral genes [J].
Haecker, SE ;
Stedman, HH ;
BaliceGordon, RJ ;
Smith, DBJ ;
Greelish, JP ;
Mitchell, MA ;
Wells, A ;
Sweeney, HL ;
Wilson, JM .
HUMAN GENE THERAPY, 1996, 7 (15) :1907-1914
[8]   Dimeric ligands define a role for transcriptional activation domains in reinitiation [J].
Ho, SN ;
Biggar, SR ;
Spencer, DM ;
Schreiber, SL ;
Crabtree, GR .
NATURE, 1996, 382 (6594) :822-826
[9]   Rapid retroviral delivery of tetracycline-inducible genes in a single autoregulatory cassette [J].
Hofmann, A ;
Nolan, GP ;
Blau, HM .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1996, 93 (11) :5185-5190
[10]   Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers [J].
Jooss, K ;
Yang, YP ;
Fisher, KJ ;
Wilson, JM .
JOURNAL OF VIROLOGY, 1998, 72 (05) :4212-4223