Best evidence on B-domain deletion and the immunogenicity of recombinant factor VIII

被引:11
作者
Aledort, L. M. [1 ]
Navickis, R. J. [2 ]
Wilkes, M. M. [2 ]
机构
[1] Mt Sinai Sch Med, New York, NY 10029 USA
[2] Hygeia Associates, Grass Valley, CA USA
关键词
PREVIOUSLY TREATED PATIENTS; PLASMA/ALBUMIN-FREE METHOD; HEMOPHILIA-A PATIENTS; CLINICAL-EVALUATION; POSTMARKETING SURVEILLANCE; FULL-LENGTH; SAFETY SURVEILLANCE; REGRESSION-ANALYSIS; HOME THERAPY; EFFICACY;
D O I
10.1111/j.1538-7836.2011.04496.x
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:2325 / 2327
页数:3
相关论文
共 37 条
[1]  
Abshire TC, 2000, THROMB HAEMOSTASIS, V83, P811
[2]   Can B-domain deletion alter the immunogenicity of recombinant factor VIII? A meta-analysis of prospective clinical studies [J].
Aledort, L. M. ;
Navickis, R. J. ;
Wilkes, M. M. .
JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2011, 9 (11) :2180-2192
[3]  
Auerswald G, 2009, J THROMB HAEMOST, V7, P524
[4]  
AygorenPursun E, 1997, THROMB HAEMOSTASIS, V78, P1352
[5]   Plasma and albumin-free recombinant factor VIII: pharmacokinetics, efficacy and safety in previously treated pediatric patients [J].
Blanchette, V. S. ;
Shapiro, A. D. ;
Liesner, R. J. ;
Navarro, F. Hernandez ;
Warrier, I. ;
Schroth, P. C. ;
Spotts, G. ;
Ewenstein, B. M. .
JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2008, 6 (08) :1319-1326
[6]   Efficacy and safety of secondary prophylactic vs. on-demand sucrose-formulated recombinant factor VIII treatment in adults with severe hemophilia A: results from a 13-month crossover study [J].
Collins, P. ;
Faradji, A. ;
Morfini, M. ;
Enriquez, M. M. ;
Schwartz, L. .
JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2010, 8 (01) :83-89
[7]  
Courter SG, 2001, SEMIN HEMATOL, V38, P44, DOI 10.1053/shem.2001.25893
[8]   An observational study of sucrose-formulated recombinant factor VIII for Japanese patients with haemophilia A [J].
Delumeau, Jean-Christophe ;
Ikegawa, Chiho ;
Yokoyama, Chisato ;
Haupt, Verena .
THROMBOSIS AND HAEMOSTASIS, 2008, 100 (01) :32-37
[9]   Efficacy assessment of a new clotting factor concentrate in haemophilia A patients, including prophylactic treatment [J].
Den Uijl, I. ;
Mauser-Bunschoten, E. P. ;
Roosendaal, G. ;
Schutgens, R. ;
Fischer, K. .
HAEMOPHILIA, 2009, 15 (06) :1215-1218
[10]  
Fukutake K, 2009, J THROMB HAEMOST, V7, P823