共 104 条
Altering the tropism of lentiviral vectors through pseudotyping
被引:375
作者:

Cronin, J
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机构:
Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA

Zhang, XY
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机构:
Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA

Reiser, J
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机构:
Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA
机构:
[1] Louisiana State Univ, Hlth Sci Ctr, Gene Therapy Program, New Orleans, LA 70112 USA
关键词:
lentiviral vector;
gene therapy;
glycoproteins;
vector tropism;
D O I:
10.2174/1566523054546224
中图分类号:
Q3 [遗传学];
学科分类号:
071007 ;
090102 ;
摘要:
The host range of retroviral vectors including lentiviral vectors can be expanded or altered by a process known as pseudotyping. Pseudotyped lentiviral vectors consist of vector particles bearing glycoproteins (GPs) derived from other enveloped viruses. Such particles possess the tropism of the virus from which the GP was derived. For example, to exploit the natural neural tropism of rabies virus, vectors designed to target the central nervous system have been pseudotyped using rabies virus-derived GPs. Among the first and still most widely used GPs for pseudotyping lentiviral vectors is the vesicular stomatitis virus GP (VSV-G), due to the very broad tropism and stability of the resulting pseudotypes. Pseudotypes involving VSV-G have become effectively the standard for evaluating the efficiency of other pseudotypes. This review samples a few of the more prominent examples from the ever-expanding list of published lentiviral pseudotypes, noting comparisons made with pseudotypes involving VSV-G in terms of titer, viral particle stability, toxicity, and host-cell specificity. Particular attention is paid to publications of successfully targeting a specific organ or cell types.
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页码:387 / 398
页数:12
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共 104 条
[1]
High-efficiency gene transfer into CD34(+) cells with a human immunodeficiency virus type 1-based retroviral vector pseudotyped with vesicular stomatitis virus envelope glycoprotein G
[J].
Akkina, RK
;
Walton, RM
;
Chen, ML
;
Li, QX
;
Planelles, V
;
Chen, ISY
.
JOURNAL OF VIROLOGY,
1996, 70 (04)
:2581-2585

Akkina, RK
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,DEPT MICROBIOL & IMMUNOL,LOS ANGELES,CA 90095

Walton, RM
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,DEPT MICROBIOL & IMMUNOL,LOS ANGELES,CA 90095

Chen, ML
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,DEPT MICROBIOL & IMMUNOL,LOS ANGELES,CA 90095

Li, QX
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,DEPT MICROBIOL & IMMUNOL,LOS ANGELES,CA 90095

Planelles, V
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,DEPT MICROBIOL & IMMUNOL,LOS ANGELES,CA 90095

Chen, ISY
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,DEPT MICROBIOL & IMMUNOL,LOS ANGELES,CA 90095
[2]
Lentivector-mediated SMN replacement in a mouse model of spinal muscular atrophy
[J].
Azzouz, M
;
Le, T
;
Ralph, GS
;
Walmsley, L
;
Monani, UR
;
Lee, DCP
;
Wilkes, F
;
Mitrophanous, KA
;
Kingsman, SM
;
Burghes, AHM
;
Mazarakis, ND
.
JOURNAL OF CLINICAL INVESTIGATION,
2004, 114 (12)
:1726-1731

Azzouz, M
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Le, T
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Ralph, GS
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Walmsley, L
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Monani, UR
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Lee, DCP
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Wilkes, F
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Mitrophanous, KA
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Kingsman, SM
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Burghes, AHM
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England

Mazarakis, ND
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMedica Plc, Medawar Ctr, Oxford OX4 4GA, England
[3]
VEGF delivery with retrogradely transported lentivector prolongs survival in a mouse ALS model
[J].
Azzouz, M
;
Ralph, GS
;
Storkebaum, E
;
Walmsley, LE
;
Mitrophanous, KA
;
Kingsman, SM
;
Carmeliet, P
;
Mazarakis, ND
.
NATURE,
2004, 429 (6990)
:413-417

Azzouz, M
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Ralph, GS
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Storkebaum, E
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Walmsley, LE
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Mitrophanous, KA
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Kingsman, SM
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Carmeliet, P
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England

Mazarakis, ND
论文数: 0 引用数: 0
h-index: 0
机构: Oxford BioMed Plc, Oxford, England
[4]
Evidence of two Lyssavirus phylogroups with distinct pathogenicity and immunogenicity
[J].
Badrane, H
;
Bahloul, C
;
Perrin, P
;
Tordo, N
.
JOURNAL OF VIROLOGY,
2001, 75 (07)
:3268-3276

Badrane, H
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France

Bahloul, C
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France

Perrin, P
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France

Tordo, N
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France Inst Pasteur, Lab Lyssavirus, Dept Virol, F-75724 Paris 15, France
[5]
Optimized lentiviral vector production and purification procedure prevents immune response after transduction of mouse brain
[J].
Baekelandt, V
;
Eggermont, K
;
Michiels, M
;
Nuttin, B
;
Debyser, Z
.
GENE THERAPY,
2003, 10 (23)
:1933-1940

Baekelandt, V
论文数: 0 引用数: 0
h-index: 0
机构: Lab Expt Neurosurg & Neuroanat, B-3000 Louvain, Belgium

Eggermont, K
论文数: 0 引用数: 0
h-index: 0
机构: Lab Expt Neurosurg & Neuroanat, B-3000 Louvain, Belgium

Michiels, M
论文数: 0 引用数: 0
h-index: 0
机构: Lab Expt Neurosurg & Neuroanat, B-3000 Louvain, Belgium

Nuttin, B
论文数: 0 引用数: 0
h-index: 0
机构: Lab Expt Neurosurg & Neuroanat, B-3000 Louvain, Belgium

Debyser, Z
论文数: 0 引用数: 0
h-index: 0
机构: Lab Expt Neurosurg & Neuroanat, B-3000 Louvain, Belgium
[6]
Human immunodeficiency virus type 1 cell cycle control: Vpr is cytostatic and mediates G(2) accumulation by a mechanism which differs from DNA damage checkpoint control
[J].
Bartz, SR
;
Rogel, ME
;
Emerman, M
.
JOURNAL OF VIROLOGY,
1996, 70 (04)
:2324-2331

Bartz, SR
论文数: 0 引用数: 0
h-index: 0
机构:
FRED HUTCHINSON CANC RES CTR,DIV MOLEC MED,SEATTLE,WA 98104 FRED HUTCHINSON CANC RES CTR,DIV MOLEC MED,SEATTLE,WA 98104

Rogel, ME
论文数: 0 引用数: 0
h-index: 0
机构:
FRED HUTCHINSON CANC RES CTR,DIV MOLEC MED,SEATTLE,WA 98104 FRED HUTCHINSON CANC RES CTR,DIV MOLEC MED,SEATTLE,WA 98104

Emerman, M
论文数: 0 引用数: 0
h-index: 0
机构:
FRED HUTCHINSON CANC RES CTR,DIV MOLEC MED,SEATTLE,WA 98104 FRED HUTCHINSON CANC RES CTR,DIV MOLEC MED,SEATTLE,WA 98104
[7]
Construction and molecular analysis of gene transfer systems derived from bovine immunodeficiency virus
[J].
Berkowitz, R
;
Ilves, H
;
Lin, WY
;
Eckert, K
;
Coward, A
;
Tamaki, S
;
Veres, G
;
Plavec, I
.
JOURNAL OF VIROLOGY,
2001, 75 (07)
:3371-3382

Berkowitz, R
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Ilves, H
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Lin, WY
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Eckert, K
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Coward, A
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Tamaki, S
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Veres, G
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA

Plavec, I
论文数: 0 引用数: 0
h-index: 0
机构:
Systemix Inc, Palo Alto, CA 94304 USA Systemix Inc, Palo Alto, CA 94304 USA
[8]
Gene transfer systems derived from visna virus: Analysis of virus production and infectivity
[J].
Berkowitz, RD
;
Ilves, H
;
Plavec, I
;
Veres, G
.
VIROLOGY,
2001, 279 (01)
:116-129

Berkowitz, RD
论文数: 0 引用数: 0
h-index: 0
机构:
SyStemix Inc, Palo Alto, CA 94304 USA SyStemix Inc, Palo Alto, CA 94304 USA

Ilves, H
论文数: 0 引用数: 0
h-index: 0
机构:
SyStemix Inc, Palo Alto, CA 94304 USA SyStemix Inc, Palo Alto, CA 94304 USA

Plavec, I
论文数: 0 引用数: 0
h-index: 0
机构:
SyStemix Inc, Palo Alto, CA 94304 USA SyStemix Inc, Palo Alto, CA 94304 USA

Veres, G
论文数: 0 引用数: 0
h-index: 0
机构:
SyStemix Inc, Palo Alto, CA 94304 USA SyStemix Inc, Palo Alto, CA 94304 USA
[9]
Oncoretrovirus and lentivirus vectors pseudotyped with lymphocytic choriomeningitis virus glycoprotein: Generation, concentration, and broad host range
[J].
Beyer, WR
;
Westphal, M
;
Ostertag, W
;
von Laer, D
.
JOURNAL OF VIROLOGY,
2002, 76 (03)
:1488-1495

Beyer, WR
论文数: 0 引用数: 0
h-index: 0
机构: Univ Hamburg, Heinrich Pette Inst Expt Virol & Immunol, D-20251 Hamburg, Germany

Westphal, M
论文数: 0 引用数: 0
h-index: 0
机构: Univ Hamburg, Heinrich Pette Inst Expt Virol & Immunol, D-20251 Hamburg, Germany

Ostertag, W
论文数: 0 引用数: 0
h-index: 0
机构: Univ Hamburg, Heinrich Pette Inst Expt Virol & Immunol, D-20251 Hamburg, Germany

论文数: 引用数:
h-index:
机构:
[10]
COMPLETE CLONING AND MOLECULAR-ORGANIZATION OF A RABIES-RELATED VIRUS, MOKOLA VIRUS
[J].
BOURHY, H
;
TORDO, N
;
LAFON, M
;
SUREAU, P
.
JOURNAL OF GENERAL VIROLOGY,
1989, 70
:2063-2074

BOURHY, H
论文数: 0 引用数: 0
h-index: 0

TORDO, N
论文数: 0 引用数: 0
h-index: 0

LAFON, M
论文数: 0 引用数: 0
h-index: 0

SUREAU, P
论文数: 0 引用数: 0
h-index: 0