Treatment of the immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome (IPEX) by allogeneic bone marrow transplantation

被引：172

作者：

Baud, O

Goulet, O

Canioni, D

Le Deist, F

Radford, I

Rieu, D

Dupuis-Girod, S

Cerf-Bensussan, N

Cavazzana-Calvo, M

Brousse, N

Fischer, A

Casanova, JL

机构：

[1] Hop Necker Enfants Malad, Unite Immunol & Hematol Pediat, INSERM, Lab Unite 429, F-75015 Paris, France

[2] Hop Necker Enfants Malad, Serv Immunol & Hematol Pediat, F-75015 Paris, France

[3] Hop Necker Enfants Malad, Serv Gastroenterol Pediat, F-75015 Paris, France

[4] Hop Necker Enfants Malad, Serv Anat Pathol, F-75015 Paris, France

[5] Hop Necker Enfants Malad, Lab Cytogenet Hematol, F-75015 Paris, France

[6] Hop Necker Enfants Malad, INSERM, Lab E9925, F-75015 Paris, France

[7] Hop Necker Enfants Malad, INSERM, Unite 550, Lab Univ Rene Descartes, F-75015 Paris, France

[8] Hop Arnaud Villeneuve, Serv Pediat 2, Montpellier, France

来源：

NEW ENGLAND JOURNAL OF MEDICINE | 2001年 / 344卷 / 23期

关键词：

D O I：

10.1056/NEJM200106073442304

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

[No abstract available]

引用

页码：1758 / 1762

页数：5

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