Gene therapy for the hemoglobin disorders: Past, present, and future

被引：32

作者：

Persons, DA ^{[1
]}

Nienhuis, AW ^{[1
]}

机构：

[1] St Jude Childrens Res Hosp, Dept Hematol & Oncol, Div Expt Hematol, Memphis, TN 38105 USA

来源：

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA | 2000年 / 97卷 / 10期

关键词：

D O I：

10.1073/pnas.97.10.5022

中图分类号：

O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];

学科分类号：

07 ; 0710 ; 09 ;

摘要：

引用

页码：5022 / 5024

页数：3

共 40 条

[1] In vivo selection of retrovirally transduced hematopoietic stem cells [J].

Allay, JA ;

Persons, DA ;

Galipeau, J ;

Riberdy, JM ;

Ashmun, RA ;

Blakley, RL ;

Sorrentino, BP .

NATURE MEDICINE, 1998, 4 (10) :1136-1143

[2] A MAJORITY OF MICE SHOW LONG-TERM EXPRESSION OF A HUMAN BETA-GLOBIN GENE AFTER RETROVIRUS TRANSFER INTO HEMATOPOIETIC STEM-CELLS [J].

BENDER, MA ;

GELINAS, RE ;

MILLER, AD .

MOLECULAR AND CELLULAR BIOLOGY, 1989, 9 (04) :1426-1434

[3] A proliferation switch for genetically modified cells [J].

Blau, CA ;

Peterson, KR ;

Drachman, JG ;

Spencer, DM .

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1997, 94 (07) :3076-3081

[4] Genetic correction of sickle cell disease: Insights using transgenic mouse models [J].

Blouin, MJ ;

Beauchemin, H ;

Wright, A ;

De Paepe, M ;

Sorette, M ;

Bleau, AM ;

Nakamoto, B ;

Ou, CN ;

Stamatoyannopoulos, G ;

Trudel, M .

NATURE MEDICINE, 2000, 6 (02) :177-182

[5]

BODINE DM, 1993, BLOOD, V82, P1975

[6] MULTIPLE MODIFICATIONS IN CIS-ELEMENTS OF THE LONG TERMINAL REPEAT OF RETROVIRAL VECTORS LEAD TO INCREASED EXPRESSION AND DECREASED DNA METHYLATION IN EMBRYONIC CARCINOMA-CELLS [J].

CHALLITA, PM ;

SKELTON, D ;

ELKHOUEIRY, A ;

YU, XJ ;

WEINBERG, K ;

KOHN, DB .

JOURNAL OF VIROLOGY, 1995, 69 (02) :748-755

[7] MOUSE MODEL OF HUMAN BETA(0) THALASSEMIA - TARGETED DELETION OF THE MOUSE BETA(MAJ)-GLOBIN AND BETA(MIN)-GLOBIN GENES IN EMBRYONIC STEM CELLS [J].

CIAVATTA, DJ ;

RYAN, TM ;

FARMER, SC ;

TOWNES, TM .

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1995, 92 (20) :9259-9263

[8]

Davis BM, 1997, CANCER RES, V57, P5093

[9] High levels of lymphoid expression of enhanced green fluorescent protein in nonhuman primates transplanted with cytokine-mobilized peripheral blood CD34+ cells [J].

Donahue, RE ;

Wersto, RP ;

Allay, JA ;

Agricola, BA ;

Metzger, ME ;

Nienhuis, AW ;

Persons, DA ;

Sorrentino, BP .

BLOOD, 2000, 95 (02) :445-452

[10] RETROVIRALLY MARKED CD34-ENRICHED PERIPHERAL-BLOOD AND BONE-MARROW CELLS CONTRIBUTE TO LONG-TERM ENGRAFTMENT AFTER AUTOLOGOUS TRANSPLANTATION [J].

DUNBAR, CE ;

COTTLERFOX, M ;

OSHAUGHNESSY, JA ;

DOREN, S ;

CARTER, C ;

BERENSON, R ;

BROWN, S ;

MOEN, RC ;

GREENBLATT, J ;

STEWART, FM ;

LEITMAN, SF ;

WILSON, WH ;

COWAN, K ;

YOUNG, NS ;

NIENHUIS, AW .

BLOOD, 1995, 85 (11) :3048-3057

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