It's all about the clothing: capsid domination in the adeno-associated viral vector world

被引：16

作者：

Arruda, V. R.

Xiao, W.

机构：

[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[2] Univ Penn, Sch Med, Dept Pediat, Philadelphia, PA 19104 USA

来源：

JOURNAL OF THROMBOSIS AND HAEMOSTASIS | 2007年 / 5卷 / 01期

关键词：

SEVERE HEMOPHILIA-B; GENE-TRANSFER; SKELETAL-MUSCLE; FACTOR-IX; IN-VIVO; VIRUS SEROTYPE-8; TRANSDUCTION; LIVER; THERAPY; DELIVERY;

D O I：

10.1111/j.1538-7836.2006.02262.x

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：12 / 15

页数：4

共 27 条

[1] Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model [J].

Arruda, VR ;

Stedman, HH ;

Nichols, TC ;

Haskins, ME ;

Nicholson, M ;

Herzog, RW ;

Couto, LB ;

High, KA .

BLOOD, 2005, 105 (09) :3458-3464

[2] Analysis of tumors arising in male B6C3F1 mice with and without AAV vector delivery to liver [J].

Bell, Peter ;

Moscioni, A. David ;

McCarter, Robert J. ;

Wu, Di ;

Gao, Guangping ;

Hoang, Albert ;

Sanmiguel, Julio C. ;

Sun, Xun ;

Wivel, Nelson A. ;

Raper, Steven E. ;

Furth, Emma E. ;

Batshaw, Mark L. ;

Wilson, James M. .

MOLECULAR THERAPY, 2006, 14 (01) :34-+

[3] Efficient myocyte gene delivery with complete cardiac surgical isolation in situ [J].

Bridges, CR ;

Gopal, K ;

Holt, DE ;

Yarnall, C ;

Cole, S ;

Anderson, RB ;

Yin, XQ ;

Nelson, A ;

Kozyak, BW ;

Wang, ZL ;

Lesniewski, J ;

Su, LT ;

Thesier, DM ;

Sundar, H ;

Stedman, HH .

JOURNAL OF THORACIC AND CARDIOVASCULAR SURGERY, 2005, 130 (05) :1364-1370

[4] Direct exposure of mouse spermatozoa to very high concentrations of a serotype-2 adeno-associated virus gene therapy vector fails to lead to germ cell transduction [J].

Couto, L ;

Parker, A ;

Gordon, JW .

HUMAN GENE THERAPY, 2004, 15 (03) :287-291

[5] Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models [J].

Davidoff, AM ;

Gray, JT ;

Ng, CYC ;

Zhang, YB ;

Zhou, JF ;

Spence, Y ;

Bakar, Y ;

Nathwani, AC .

MOLECULAR THERAPY, 2005, 11 (06) :875-888

[6] Identification of PDGFR as a receptor for AAV-5 transduction [J].

Di Pasquale, G ;

Davidson, BL ;

Stein, CS ;

Martins, IS ;

Scudiero, D ;

Monks, A ;

Chiorini, JA .

NATURE MEDICINE, 2003, 9 (10) :1306-1312

[7] Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy [J].

Gao, GP ;

Alvira, MR ;

Wang, LL ;

Calcedo, R ;

Johnston, J ;

Wilson, JM .

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2002, 99 (18) :11854-11859

[8] Systemic delivery of genes to striated muscles using adeno-associated viral vectors [J].

Gregorevic, P ;

Blankinship, MJ ;

Allen, JM ;

Crawford, RW ;

Meuse, L ;

Miller, DG ;

Russell, DW ;

Chamberlain, JS .

NATURE MEDICINE, 2004, 10 (08) :828-834

[9] Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy [J].

Grimm, D ;

Zhou, SZ ;

Nakai, H ;

Thomas, CE ;

Storm, TA ;

Fuess, S ;

Matsushita, T ;

Allen, J ;

Surosky, R ;

Lochrie, M ;

Meuse, L ;

McClelland, A ;

Colosi, P ;

Kay, MA .

BLOOD, 2003, 102 (07) :2412-2419

[10] Liver transduction with recombinant adeno-associated virus is primarily restricted by capsid serotype not vector genotype [J].

Grimm, D ;

Pandey, K ;

Nakai, H ;

Storm, TA ;

Kay, MA .

JOURNAL OF VIROLOGY, 2006, 80 (01) :426-439

← 1 2 3 →