Early marrow transplantation in a pre-symptomatic neonate with late infantile metachromatic leukodystrophy does not halt disease progression

被引：41

作者：

Bredius, R. G. M. ^{[1
]}

Laan, L. A. E. M.

Lankester, A. C.

Poorthuis, B. J. H. M.

van Tol, M. J. D.

Egeler, R. M.

Arts, W. F. M.

机构：

[1] Leiden Univ, Med Ctr, Dept Pediat, NL-2300 RA Leiden, Netherlands

[2] Leiden Univ, Med Ctr, Dept Neurol, NL-2300 RA Leiden, Netherlands

[3] Univ Amsterdam, Acad Med Ctr, Dept Med Biochem, NL-1105 AZ Amsterdam, Netherlands

[4] Erasmus MC, Sophia Childrens Hosp, Dept Pediat Neurol, Rotterdam, Netherlands

来源：

BONE MARROW TRANSPLANTATION | 2007年 / 39卷 / 05期

关键词：

D O I：

10.1038/sj.bmt.1705581

中图分类号：

Q6 [生物物理学];

学科分类号：

071011 ;

摘要：

引用

页码：309 / 310

页数：2

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[5]

Von Figura K, 2001, METABOLIC MOL BASES, P3695

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