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Gene therapy - The best of times, the worst of times
被引:48
作者
:
Anderson, WF
论文数:
0
引用数:
0
h-index:
0
机构:
Univ So Calif, Keck Sch Med, Norris Canc Ctr, Los Angeles, CA 90033 USA
Univ So Calif, Keck Sch Med, Norris Canc Ctr, Los Angeles, CA 90033 USA
Anderson, WF
[
1
]
机构
:
[1]
Univ So Calif, Keck Sch Med, Norris Canc Ctr, Los Angeles, CA 90033 USA
来源
:
SCIENCE
|
2000年
/ 288卷
/ 5466期
关键词
:
D O I
:
10.1126/science.288.5466.627
中图分类号
:
O [数理科学和化学];
P [天文学、地球科学];
Q [生物科学];
N [自然科学总论];
学科分类号
:
07
[理学]
;
0710
[生物学]
;
09
[农学]
;
摘要
:
[No abstract available]
引用
收藏
页码:627 / +
页数:2
相关论文
共 11 条
[1]
HUMAN GENE-THERAPY
[J].
ANDERSON, WF
论文数:
0
引用数:
0
h-index:
0
ANDERSON, WF
.
SCIENCE,
1992,
256
(5058)
:808
-813
[2]
T-LYMPHOCYTE-DIRECTED GENE-THERAPY FOR ADA(-) SCID - INITIAL TRIAL RESULTS AFTER 4 YEARS
[J].
BLAESE, RM
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
BLAESE, RM
;
CULVER, KW
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CULVER, KW
;
MILLER, AD
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MILLER, AD
;
CARTER, CS
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CARTER, CS
;
FLEISHER, T
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
FLEISHER, T
;
CLERICI, M
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CLERICI, M
;
SHEARER, G
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
SHEARER, G
;
CHANG, L
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CHANG, L
;
CHIANG, YW
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CHIANG, YW
;
TOLSTOSHEV, P
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
TOLSTOSHEV, P
;
GREENBLATT, JJ
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
GREENBLATT, JJ
;
ROSENBERG, SA
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
ROSENBERG, SA
;
KLEIN, H
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
KLEIN, H
;
BERGER, M
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
BERGER, M
;
MULLEN, CA
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MULLEN, CA
;
RAMSEY, WJ
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
RAMSEY, WJ
;
MUUL, L
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MUUL, L
;
MORGAN, RA
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MORGAN, RA
;
ANDERSON, WF
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
ANDERSON, WF
.
SCIENCE,
1995,
270
(5235)
:475
-480
[3]
GENE-THERAPY IN PERIPHERAL-BLOOD LYMPHOCYTES AND BONE-MARROW FOR ADA(-) IMMUNODEFICIENT PATIENTS
[J].
BORDIGNON, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
BORDIGNON, C
;
NOTARANGELO, LD
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
NOTARANGELO, LD
;
NOBILI, N
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
NOBILI, N
;
FERRARI, G
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
FERRARI, G
;
CASORATI, G
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
CASORATI, G
;
PANINA, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
PANINA, P
;
MAZZOLARI, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
MAZZOLARI, E
;
MAGGIONI, D
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
MAGGIONI, D
;
ROSSI, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
ROSSI, C
;
SERVIDA, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
SERVIDA, P
;
论文数:
引用数:
h-index:
机构:
UGAZIO, AG
;
MAVILIO, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
MAVILIO, F
.
SCIENCE,
1995,
270
(5235)
:470
-475
[4]
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
[J].
Cavazzana-Calvo, M
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Cavazzana-Calvo, M
;
Hacein-Bey, S
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Hacein-Bey, S
;
Basile, CD
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Basile, CD
;
Gross, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Gross, F
;
Yvon, E
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Yvon, E
;
Nusbaum, P
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Nusbaum, P
;
Selz, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Selz, F
;
Hue, C
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Hue, C
;
Certain, S
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Certain, S
;
Casanova, JL
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Casanova, JL
;
论文数:
引用数:
h-index:
机构:
Bousso, P
;
Le Deist, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Le Deist, F
;
Fischer, A
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Fischer, A
.
SCIENCE,
2000,
288
(5466)
:669
-672
[5]
Hoogerbrugge PM, 1996, GENE THER, V3, P179
[6]
Angiogenesis and vasculogenesis as therapeutic strategies for postnatal neovascularization
[J].
论文数:
引用数:
h-index:
机构:
Isner, JM
;
Asahara, T
论文数:
0
引用数:
0
h-index:
0
机构:
St Elizabeths Med Ctr, Div Vasc Med, Boston, MA 02135 USA
Asahara, T
.
JOURNAL OF CLINICAL INVESTIGATION,
1999,
103
(09)
:1231
-1236
[7]
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
[J].
Kay, MA
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Kay, MA
;
Manno, CS
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Manno, CS
;
Ragni, MV
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Ragni, MV
;
Larson, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Larson, PJ
;
Couto, LB
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Couto, LB
;
论文数:
引用数:
h-index:
机构:
McClelland, A
;
Glader, B
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Glader, B
;
Chew, AJ
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Chew, AJ
;
Tai, SJ
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Tai, SJ
;
Herzog, RW
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Herzog, RW
;
Arruda, V
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Arruda, V
;
Johnson, F
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Johnson, F
;
Scallan, C
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Scallan, C
;
Skarsgard, E
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Skarsgard, E
;
Flake, AW
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Flake, AW
;
High, KA
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
High, KA
.
NATURE GENETICS,
2000,
24
(03)
:257
-261
[8]
ENGRAFTMENT OF GENE-MODIFIED UMBILICAL-CORD BLOOD-CELLS IN NEONATES WITH ADENOSINE-DEAMINASE DEFICIENCY
[J].
KOHN, DB
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
KOHN, DB
;
WEINBERG, KI
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WEINBERG, KI
;
NOLTA, JA
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
NOLTA, JA
;
HEISS, LN
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
HEISS, LN
;
LENARSKY, C
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
LENARSKY, C
;
CROOKS, GM
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
CROOKS, GM
;
HANLEY, ME
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
HANLEY, ME
;
ANNETT, G
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
ANNETT, G
;
BROOKS, JS
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BROOKS, JS
;
ELKHOUREIY, A
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
ELKHOUREIY, A
;
LAWRENCE, K
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
LAWRENCE, K
;
WELLS, S
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WELLS, S
;
MOEN, RC
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
MOEN, RC
;
BASTIAN, J
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BASTIAN, J
;
WILLIAMSHERMAN, DE
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WILLIAMSHERMAN, DE
;
ELDER, M
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
ELDER, M
;
WARA, D
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WARA, D
;
BOWEN, T
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BOWEN, T
;
HERSHFIELD, MS
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
HERSHFIELD, MS
;
MULLEN, CA
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
MULLEN, CA
;
BLAESE, RM
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BLAESE, RM
;
PARKMAN, R
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
PARKMAN, R
.
NATURE MEDICINE,
1995,
1
(10)
:1017
-1023
[9]
T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates
[J].
Kohn, DB
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Kohn, DB
;
Hershfield, MS
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Hershfield, MS
;
Carbonaro, D
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Carbonaro, D
;
Shigeoka, A
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Shigeoka, A
;
Brooks, J
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Brooks, J
;
Smogorzewska, EM
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Smogorzewska, EM
;
Barsky, LW
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Barsky, LW
;
Chan, R
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Chan, R
;
Burotto, F
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Burotto, F
;
Annett, G
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Annett, G
;
Nolta, JA
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Nolta, JA
;
Crooks, G
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Crooks, G
;
Kapoor, N
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Kapoor, N
;
Elder, M
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Elder, M
;
Wara, D
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Wara, D
;
Bowen, T
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Bowen, T
;
Madsen, E
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Madsen, E
;
Snyder, FF
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Snyder, FF
;
Bastian, J
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Bastian, J
;
Muul, L
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Muul, L
;
Blaese, RM
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Blaese, RM
;
Weinberg, K
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Weinberg, K
;
Parkman, R
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Parkman, R
.
NATURE MEDICINE,
1998,
4
(07)
:775
-780
[10]
Molecular analysis of T lymphocyte-directed gene therapy for adenosine deaminase deficiency: Long-term expression in vivo of genes introduced with a retroviral vector
[J].
Mullen, CA
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Mullen, CA
;
Snitzer, K
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Snitzer, K
;
Culver, KW
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Culver, KW
;
Morgan, RA
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Morgan, RA
;
Anderson, WF
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Anderson, WF
;
Blaese, RM
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Blaese, RM
.
HUMAN GENE THERAPY,
1996,
7
(09)
:1123
-1129
←
1
2
→
共 11 条
[1]
HUMAN GENE-THERAPY
[J].
ANDERSON, WF
论文数:
0
引用数:
0
h-index:
0
ANDERSON, WF
.
SCIENCE,
1992,
256
(5058)
:808
-813
[2]
T-LYMPHOCYTE-DIRECTED GENE-THERAPY FOR ADA(-) SCID - INITIAL TRIAL RESULTS AFTER 4 YEARS
[J].
BLAESE, RM
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
BLAESE, RM
;
CULVER, KW
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CULVER, KW
;
MILLER, AD
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MILLER, AD
;
CARTER, CS
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CARTER, CS
;
FLEISHER, T
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
FLEISHER, T
;
CLERICI, M
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CLERICI, M
;
SHEARER, G
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
SHEARER, G
;
CHANG, L
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CHANG, L
;
CHIANG, YW
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
CHIANG, YW
;
TOLSTOSHEV, P
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
TOLSTOSHEV, P
;
GREENBLATT, JJ
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
GREENBLATT, JJ
;
ROSENBERG, SA
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
ROSENBERG, SA
;
KLEIN, H
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
KLEIN, H
;
BERGER, M
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
BERGER, M
;
MULLEN, CA
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MULLEN, CA
;
RAMSEY, WJ
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
RAMSEY, WJ
;
MUUL, L
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MUUL, L
;
MORGAN, RA
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
MORGAN, RA
;
ANDERSON, WF
论文数:
0
引用数:
0
h-index:
0
机构:
NCI, BETHESDA, MD 20892 USA
ANDERSON, WF
.
SCIENCE,
1995,
270
(5235)
:475
-480
[3]
GENE-THERAPY IN PERIPHERAL-BLOOD LYMPHOCYTES AND BONE-MARROW FOR ADA(-) IMMUNODEFICIENT PATIENTS
[J].
BORDIGNON, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
BORDIGNON, C
;
NOTARANGELO, LD
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
NOTARANGELO, LD
;
NOBILI, N
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
NOBILI, N
;
FERRARI, G
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
FERRARI, G
;
CASORATI, G
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
CASORATI, G
;
PANINA, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
PANINA, P
;
MAZZOLARI, E
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
MAZZOLARI, E
;
MAGGIONI, D
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
MAGGIONI, D
;
ROSSI, C
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
ROSSI, C
;
SERVIDA, P
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
SERVIDA, P
;
论文数:
引用数:
h-index:
机构:
UGAZIO, AG
;
MAVILIO, F
论文数:
0
引用数:
0
h-index:
0
机构:
UNIV BRESCIA, SCH MED, DEPT PEDIAT, BRESCIA, ITALY
MAVILIO, F
.
SCIENCE,
1995,
270
(5235)
:470
-475
[4]
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
[J].
Cavazzana-Calvo, M
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Cavazzana-Calvo, M
;
Hacein-Bey, S
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Hacein-Bey, S
;
Basile, CD
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Basile, CD
;
Gross, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Gross, F
;
Yvon, E
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Yvon, E
;
Nusbaum, P
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Nusbaum, P
;
Selz, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Selz, F
;
Hue, C
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Hue, C
;
Certain, S
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Certain, S
;
Casanova, JL
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Casanova, JL
;
论文数:
引用数:
h-index:
机构:
Bousso, P
;
Le Deist, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Le Deist, F
;
Fischer, A
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Fischer, A
.
SCIENCE,
2000,
288
(5466)
:669
-672
[5]
Hoogerbrugge PM, 1996, GENE THER, V3, P179
[6]
Angiogenesis and vasculogenesis as therapeutic strategies for postnatal neovascularization
[J].
论文数:
引用数:
h-index:
机构:
Isner, JM
;
Asahara, T
论文数:
0
引用数:
0
h-index:
0
机构:
St Elizabeths Med Ctr, Div Vasc Med, Boston, MA 02135 USA
Asahara, T
.
JOURNAL OF CLINICAL INVESTIGATION,
1999,
103
(09)
:1231
-1236
[7]
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
[J].
Kay, MA
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Kay, MA
;
Manno, CS
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Manno, CS
;
Ragni, MV
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Ragni, MV
;
Larson, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Larson, PJ
;
Couto, LB
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Couto, LB
;
论文数:
引用数:
h-index:
机构:
McClelland, A
;
Glader, B
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Glader, B
;
Chew, AJ
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Chew, AJ
;
Tai, SJ
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Tai, SJ
;
Herzog, RW
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Herzog, RW
;
Arruda, V
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Arruda, V
;
Johnson, F
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Johnson, F
;
Scallan, C
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Scallan, C
;
Skarsgard, E
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Skarsgard, E
;
Flake, AW
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Flake, AW
;
High, KA
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
High, KA
.
NATURE GENETICS,
2000,
24
(03)
:257
-261
[8]
ENGRAFTMENT OF GENE-MODIFIED UMBILICAL-CORD BLOOD-CELLS IN NEONATES WITH ADENOSINE-DEAMINASE DEFICIENCY
[J].
KOHN, DB
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
KOHN, DB
;
WEINBERG, KI
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WEINBERG, KI
;
NOLTA, JA
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
NOLTA, JA
;
HEISS, LN
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
HEISS, LN
;
LENARSKY, C
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
LENARSKY, C
;
CROOKS, GM
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
CROOKS, GM
;
HANLEY, ME
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
HANLEY, ME
;
ANNETT, G
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
ANNETT, G
;
BROOKS, JS
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BROOKS, JS
;
ELKHOUREIY, A
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
ELKHOUREIY, A
;
LAWRENCE, K
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
LAWRENCE, K
;
WELLS, S
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WELLS, S
;
MOEN, RC
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
MOEN, RC
;
BASTIAN, J
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BASTIAN, J
;
WILLIAMSHERMAN, DE
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WILLIAMSHERMAN, DE
;
ELDER, M
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
ELDER, M
;
WARA, D
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
WARA, D
;
BOWEN, T
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BOWEN, T
;
HERSHFIELD, MS
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
HERSHFIELD, MS
;
MULLEN, CA
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
MULLEN, CA
;
BLAESE, RM
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
BLAESE, RM
;
PARKMAN, R
论文数:
0
引用数:
0
h-index:
0
机构:
GENET THERAPY INC,GAITHERSBURG,MD 20878
PARKMAN, R
.
NATURE MEDICINE,
1995,
1
(10)
:1017
-1023
[9]
T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates
[J].
Kohn, DB
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Kohn, DB
;
Hershfield, MS
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Hershfield, MS
;
Carbonaro, D
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Carbonaro, D
;
Shigeoka, A
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Shigeoka, A
;
Brooks, J
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Brooks, J
;
Smogorzewska, EM
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Smogorzewska, EM
;
Barsky, LW
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Barsky, LW
;
Chan, R
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Chan, R
;
Burotto, F
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Burotto, F
;
Annett, G
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Annett, G
;
Nolta, JA
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Nolta, JA
;
Crooks, G
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Crooks, G
;
Kapoor, N
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Kapoor, N
;
Elder, M
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Elder, M
;
Wara, D
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Wara, D
;
Bowen, T
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Bowen, T
;
Madsen, E
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Madsen, E
;
Snyder, FF
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Snyder, FF
;
Bastian, J
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Bastian, J
;
Muul, L
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Muul, L
;
Blaese, RM
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Blaese, RM
;
Weinberg, K
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Weinberg, K
;
Parkman, R
论文数:
0
引用数:
0
h-index:
0
机构:
Childrens Hosp Los Angeles, Div Immunol Res Bone Marrow Transplantat, Los Angeles, CA 90027 USA
Parkman, R
.
NATURE MEDICINE,
1998,
4
(07)
:775
-780
[10]
Molecular analysis of T lymphocyte-directed gene therapy for adenosine deaminase deficiency: Long-term expression in vivo of genes introduced with a retroviral vector
[J].
Mullen, CA
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Mullen, CA
;
Snitzer, K
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Snitzer, K
;
Culver, KW
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Culver, KW
;
Morgan, RA
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Morgan, RA
;
Anderson, WF
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Anderson, WF
;
Blaese, RM
论文数:
0
引用数:
0
h-index:
0
机构:
NIH,NATL CTR HUMAN GENOME RES,CLIN GENE THERAPY BRANCH,BETHESDA,MD 20892
Blaese, RM
.
HUMAN GENE THERAPY,
1996,
7
(09)
:1123
-1129
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