Promises and challenges of genetic therapy for blindness

被引：5

作者：

Cremers, Frans P. M. ^{[1
,2
]}

Collin, Rob W. J. ^{[1
,2
,3
]}

机构：

[1] Radboud Univ Nijmegen, Med Ctr, Dept Human Genet, NL-6500 HB Nijmegen, Netherlands

[2] Radboud Univ Nijmegen, Med Ctr, Nijmegen Ctr Mol Life Sci, NL-6500 HB Nijmegen, Netherlands

[3] Radboud Univ Nijmegen, Med Ctr, Dept Ophthalmol, NL-6500 HB Nijmegen, Netherlands

来源：

LANCET | 2009年 / 374卷 / 9701期

关键词：

LEBERS CONGENITAL AMAUROSIS; VISION; MUTATIONS; SCID-X1; MODEL; ROD;

D O I：

10.1016/S0140-6736(09)61869-9

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：1569 / 1570

页数：2

共 12 条

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LANCET, 2009, 374 (9701) :1597-1605

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