Lessons Learned from the Clinical Development and Market Authorization of Glybera

被引：110

作者：

Bryant, Laura M. ^{[1
]}

Christopher, Devin M. ^{[2
]}

Giles, April R. ^{[2
]}

Hinderer, Christian ^{[2
]}

Rodriguez, Jesse L. ^{[2
]}

Smith, Jenessa B. ^{[2
]}

Traxler, Elizabeth A. ^{[2
]}

Tycko, Josh ^{[2
]}

Wojno, Adam P.

Wilson, James M. ^{[2
]}

机构：

[1] Univ Penn, Neurosci Grad Grp, Philadelphia, PA 19104 USA

[2] Univ Penn, Cell & Mol Biol Grad Grp, Gene Therapy & Vaccines Program, Philadelphia, PA 19104 USA

来源：

HUMAN GENE THERAPY CLINICAL DEVELOPMENT | 2013年 / 24卷 / 02期

基金：

比尔及梅琳达.盖茨基金会;

关键词：

LIPOPROTEIN-LIPASE DEFICIENCY; GENE-TRANSFER; FACTOR-IX; THERAPY;

D O I：

10.1089/humc.2013.087

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

[No abstract available]

引用

页码：55 / 64

页数：10

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