共 15 条
[1]
Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning
[J].
Aiuti, A
;
Slavin, S
;
Aker, M
;
Ficara, F
;
Deola, S
;
Mortellaro, A
;
Morecki, S
;
Andolfi, G
;
Tabucchi, A
;
Carlucci, F
;
Marinello, E
;
Cattaneo, F
;
Vai, S
;
Servida, P
;
Miniero, R
;
Roncarolo, MG
;
Bordignon, C
.
SCIENCE,
2002, 296 (5577)
:2410-2413

Aiuti, A
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Slavin, S
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Aker, M
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Ficara, F
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Deola, S
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Mortellaro, A
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Morecki, S
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Andolfi, G
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Tabucchi, A
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Carlucci, F
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Marinello, E
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Cattaneo, F
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Vai, S
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Servida, P
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Miniero, R
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Roncarolo, MG
论文数: 0 引用数: 0
h-index: 0
机构: San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

Bordignon, C
论文数: 0 引用数: 0
h-index: 0
机构:
San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
[2]
CARTIER N, 2007, 15 ANN C EUR SOC GEN
[3]
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
[J].
Cavazzana-Calvo, M
;
Hacein-Bey, S
;
Basile, CD
;
Gross, F
;
Yvon, E
;
Nusbaum, P
;
Selz, F
;
Hue, C
;
Certain, S
;
Casanova, JL
;
Bousso, P
;
Le Deist, F
;
Fischer, A
.
SCIENCE,
2000, 288 (5466)
:669-672

Cavazzana-Calvo, M
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Hacein-Bey, S
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Basile, CD
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Gross, F
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Yvon, E
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Nusbaum, P
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Selz, F
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Hue, C
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Certain, S
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Casanova, JL
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

论文数: 引用数:
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机构:

Le Deist, F
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France

Fischer, A
论文数: 0 引用数: 0
h-index: 0
机构: Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
[4]
Stem Cell Marking With Promotor-deprived Self-inactivating Retroviral Vectors Does Not Lead to Induced Clonal Imbalance
[J].
Cornils, Kerstin
;
Lange, Claudia
;
Schambach, Axel
;
Brugman, Martijn H.
;
Nowak, Regine
;
Lioznov, Michael
;
Baum, Christopher
;
Fehse, Boris
.
MOLECULAR THERAPY,
2009, 17 (01)
:131-143

Cornils, Kerstin
论文数: 0 引用数: 0
h-index: 0
机构:
Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany
Univ Med Ctr Hamburg Eppendorf, Univ Canc Ctr, Clin Stem Cell Transplantat, Hamburg, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Lange, Claudia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Hamburg Eppendorf, Univ Canc Ctr, Clin Stem Cell Transplantat, Hamburg, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Schambach, Axel
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Expt Hematol, D-3000 Hannover, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Brugman, Martijn H.
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Expt Hematol, D-3000 Hannover, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Nowak, Regine
论文数: 0 引用数: 0
h-index: 0
机构:
Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Lioznov, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Hamburg Eppendorf, Univ Canc Ctr, Clin Stem Cell Transplantat, Hamburg, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Baum, Christopher
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Expt Hematol, D-3000 Hannover, Germany
Cincinnati Childrens Hosp, Med Ctr, Div Expt Hematol, Cincinnati, OH USA Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany

Fehse, Boris
论文数: 0 引用数: 0
h-index: 0
机构:
Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany Goethe Univ Frankfurt, Univ Hosp, Pediat Clin 3, D-60590 Frankfurt, Germany
[5]
Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector
[J].
Gaspar, HB
;
Parsley, KL
;
Howe, S
;
King, D
;
Gilmour, KC
;
Sinclair, J
;
Brouns, G
;
Schmidt, M
;
Von Kalle, C
;
Barington, T
;
Jakobsen, MA
;
Christensen, HO
;
Al Ghonaium, A
;
White, HN
;
Smith, JL
;
Levinsky, RJ
;
Ali, RR
;
Kinnon, C
;
Thrasher, AJ
.
LANCET,
2004, 364 (9452)
:2181-2187

Gaspar, HB
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Parsley, KL
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Howe, S
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

King, D
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Gilmour, KC
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Sinclair, J
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Brouns, G
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Schmidt, M
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Von Kalle, C
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Barington, T
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Jakobsen, MA
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Christensen, HO
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Al Ghonaium, A
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

White, HN
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Smith, JL
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Levinsky, RJ
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Ali, RR
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Kinnon, C
论文数: 0 引用数: 0
h-index: 0
机构: UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England

Thrasher, AJ
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England UCL, Inst Child Hlth, Mol Immunol Unit, London WC1N 1EH, England
[6]
LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1
[J].
Hacein-Bey-Abina, S
;
Von Kalle, C
;
Schmidt, M
;
McCcormack, MP
;
Wulffraat, N
;
Leboulch, P
;
Lim, A
;
Osborne, CS
;
Pawliuk, R
;
Morillon, E
;
Sorensen, R
;
Forster, A
;
Fraser, P
;
Cohen, JI
;
de Saint Basile, G
;
Alexander, I
;
Wintergerst, U
;
Frebourg, T
;
Aurias, A
;
Stoppa-Lyonnet, D
;
Romana, S
;
Radford-Weiss, I
;
Gross, F
;
Valensi, F
;
Delabesse, E
;
Macintyre, E
;
Sigaux, F
;
Soulier, J
;
Leiva, LE
;
Wissler, M
;
Prinz, C
;
Rabbitts, TH
;
Le Deist, F
;
Fischer, A
;
Cavazzana-Calvo, M
.
SCIENCE,
2003, 302 (5644)
:415-419

Hacein-Bey-Abina, S
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Von Kalle, C
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Schmidt, M
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

McCcormack, MP
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Wulffraat, N
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Leboulch, P
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Lim, A
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Osborne, CS
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Pawliuk, R
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Morillon, E
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Sorensen, R
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Forster, A
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Fraser, P
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Cohen, JI
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

de Saint Basile, G
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Alexander, I
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Wintergerst, U
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Frebourg, T
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Aurias, A
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Stoppa-Lyonnet, D
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Romana, S
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Radford-Weiss, I
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Gross, F
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Valensi, F
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Delabesse, E
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Macintyre, E
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Sigaux, F
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Soulier, J
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Leiva, LE
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Wissler, M
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Prinz, C
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Rabbitts, TH
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Le Deist, F
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France

Fischer, A
论文数: 0 引用数: 0
h-index: 0
机构:
INSERM, U429, F-75743 Paris 15, France INSERM, U429, F-75743 Paris 15, France

Cavazzana-Calvo, M
论文数: 0 引用数: 0
h-index: 0
机构: INSERM, U429, F-75743 Paris 15, France
[7]
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
[J].
Hacein-Bey-Abina, Salima
;
Garrigue, Alexandrine
;
Wang, Gary P.
;
Soulier, Jean
;
Lim, Annick
;
Morillon, Estelle
;
Clappier, Emmanuelle
;
Caccavelli, Laure
;
Delabesse, Eric
;
Beldjord, Kheira
;
Asnafi, Vahid
;
Macintyre, Elizabeth
;
Dal Cortivo, Liliane
;
Radford, Isabelle
;
Brousse, Nicole
;
Sigaux, Francois
;
Moshous, Despina
;
Hauer, Julia
;
Borkhardt, Arndt
;
Belohradsky, Bernd H.
;
Wintergerst, Uwe
;
Velez, Maria C.
;
Leiva, Lily
;
Sorensen, Ricardo
;
Wulffraat, Nicolas
;
Blanche, Stephane
;
Bushman, Frederic D.
;
Fischer, Alain
;
Cavazzana-Calvo, Marina
.
JOURNAL OF CLINICAL INVESTIGATION,
2008, 118 (09)
:3132-3142

Hacein-Bey-Abina, Salima
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France
Grp Hosp Univ Ouest, Ctr Invest Clin Integre Biotherapies, INSERM, Paris, France
Univ Paris 05, U768, INSERM, Paris, France
Hop Necker Enfants Malad, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

论文数: 引用数:
h-index:
机构:

Wang, Gary P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Sch Med, Dept Microbiol, Philadelphia, PA 19104 USA Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Soulier, Jean
论文数: 0 引用数: 0
h-index: 0
机构: Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Lim, Annick
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Pasteur, Dept Immunol, Unite Dev Lymphocytes, F-75724 Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Morillon, Estelle
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 05, U768, INSERM, Paris, France
Hop Necker Enfants Malad, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

论文数: 引用数:
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论文数: 引用数:
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Delabesse, Eric
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Purpan, Ctr Physiopathol Toulouse Purpan, Hematol Lab, Toulouse, France
Univ Hosp Purpan, Ctr Physiopathol Toulouse Purpan, U563, INSERM, Toulouse, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Beldjord, Kheira
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, Hematol Lab, Paris, France
Hop Necker Enfants Malad, AP HP, EMIU0210, INSERM, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Asnafi, Vahid
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, Hematol Lab, Paris, France
Hop Necker Enfants Malad, AP HP, EMIU0210, INSERM, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Macintyre, Elizabeth
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, Hematol Lab, Paris, France
Hop Necker Enfants Malad, AP HP, EMIU0210, INSERM, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Dal Cortivo, Liliane
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France
Grp Hosp Univ Ouest, Ctr Invest Clin Integre Biotherapies, INSERM, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Radford, Isabelle
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, EMIU0210, INSERM, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Brousse, Nicole
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, Dept Pathol, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Sigaux, Francois
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 07, IUH, Paris, France
Hop St Louis, AP HP, Hematol Lab, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Moshous, Despina
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, Dept Pediat Immunohematol, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Hauer, Julia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 05, U768, INSERM, Paris, France
Hop Necker Enfants Malad, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Borkhardt, Arndt
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Dusseldorf, Dept Pediat Hematol Oncol & Clin Immunol, Dusseldorf, Germany Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Belohradsky, Bernd H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Childrens Hosp Munich, Dept Infect Dis & Immunol, Munich, Germany Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Wintergerst, Uwe
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Childrens Hosp Munich, Dept Infect Dis & Immunol, Munich, Germany Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Velez, Maria C.
论文数: 0 引用数: 0
h-index: 0
机构:
Louisiana State Univ, Hlth Sci Ctr, Dept Pediat, New Orleans, LA USA Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Leiva, Lily
论文数: 0 引用数: 0
h-index: 0
机构:
Louisiana State Univ, Hlth Sci Ctr, Dept Pediat, New Orleans, LA USA Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Sorensen, Ricardo
论文数: 0 引用数: 0
h-index: 0
机构:
Louisiana State Univ, Hlth Sci Ctr, Dept Pediat, New Orleans, LA USA Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Wulffraat, Nicolas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Ctr Utrecht, Immunol Sect, Dept Pediat, Utrecht, Netherlands Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Blanche, Stephane
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, AP HP, Dept Pediat Immunohematol, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Bushman, Frederic D.
论文数: 0 引用数: 0
h-index: 0
机构: Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Fischer, Alain
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 05, U768, INSERM, Paris, France
Hop Necker Enfants Malad, Paris, France
Hop Necker Enfants Malad, AP HP, Dept Pediat Immunohematol, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France

Cavazzana-Calvo, Marina
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France
Grp Hosp Univ Ouest, Ctr Invest Clin Integre Biotherapies, INSERM, Paris, France
Univ Paris 05, U768, INSERM, Paris, France
Hop Necker Enfants Malad, Paris, France Univ Paris 05, Hop Necker Enfants Malad, AP HP, Dept Biotherapy, F-75015 Paris, France
[8]
Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients
[J].
Howe, Steven J.
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Mansour, Marc R.
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Schwarzwaelder, Kerstin
;
Bartholomae, Cynthia
;
Hubank, Michael
;
Kempski, Helena
;
Brugman, Martijn H.
;
Pike-Overzet, Karin
;
Chatters, Stephen J.
;
de Ridder, Dick
;
Gilmour, Kimberly C.
;
Adams, Stuart
;
Thornhill, Susannah I.
;
Parsley, Kathryn L.
;
Staal, Frank J. T.
;
Gale, Rosemary E.
;
Linch, David C.
;
Bayford, Jinhua
;
Brown, Lucie
;
Quaye, Michelle
;
Kinnon, Christine
;
Ancliff, Philip
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Webb, David K.
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Schmidt, Manfred
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von Kalle, Christof
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Gaspar, H. Bobby
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Thrasher, Adrian J.
.
JOURNAL OF CLINICAL INVESTIGATION,
2008, 118 (09)
:3143-3150

Howe, Steven J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Mansour, Marc R.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dept Haematol, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Schwarzwaelder, Kerstin
论文数: 0 引用数: 0
h-index: 0
机构:
German Canc Res Ctr, Natl Ctr Tumor Dis, D-6900 Heidelberg, Germany UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Bartholomae, Cynthia
论文数: 0 引用数: 0
h-index: 0
机构:
German Canc Res Ctr, Natl Ctr Tumor Dis, D-6900 Heidelberg, Germany UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Hubank, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Haematol & Canc Biol Unit, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Kempski, Helena
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Haematol & Canc Biol Unit, London, England
Great Ormond St Hosp Sick Children, Paediat Malignancy Cytogenet Unit, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Brugman, Martijn H.
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Expt Hematol, D-3000 Hannover, Germany UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Pike-Overzet, Karin
论文数: 0 引用数: 0
h-index: 0
机构:
Erasmus MC, Dept Immunol, Rotterdam, Netherlands UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Chatters, Stephen J.
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, Paediat Malignancy Cytogenet Unit, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

de Ridder, Dick
论文数: 0 引用数: 0
h-index: 0
机构:
Erasmus MC, Dept Immunol, Rotterdam, Netherlands
Delft Univ Technol, Fac Elect Engn Math & Comp Sci, Informat & Commun Theory Grp, Delft, Netherlands UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Gilmour, Kimberly C.
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Adams, Stuart
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Thornhill, Susannah I.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Parsley, Kathryn L.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Staal, Frank J. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Erasmus MC, Dept Immunol, Rotterdam, Netherlands UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Gale, Rosemary E.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dept Haematol, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Linch, David C.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dept Haematol, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Bayford, Jinhua
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Brown, Lucie
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Quaye, Michelle
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Kinnon, Christine
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Ancliff, Philip
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Webb, David K.
论文数: 0 引用数: 0
h-index: 0
机构:
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Schmidt, Manfred
论文数: 0 引用数: 0
h-index: 0
机构:
German Canc Res Ctr, Natl Ctr Tumor Dis, D-6900 Heidelberg, Germany UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

von Kalle, Christof
论文数: 0 引用数: 0
h-index: 0
机构:
German Canc Res Ctr, Natl Ctr Tumor Dis, D-6900 Heidelberg, Germany
Cincinnati Childrens Res Fdn, Div Expt Hematol & Canc Biol, Cincinnati, OH USA UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Gaspar, H. Bobby
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England

Thrasher, Adrian J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England
Great Ormond St Hosp Sick Children, London, England UCL, Inst Child Hlth, Mol Immunol Unit, Ctr Immunodeficiency, London WC1N 1EH, England
[9]
Clonal dominance of hematopoietic stem cells triggered by retroviral gene marking
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Kustikova, O
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Fehse, B
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Modlich, U
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Yang, M
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Düllmann, J
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Kamino, K
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von Neuhoff, N
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Schlegelberger, B
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Li, ZX
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Baum, C
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SCIENCE,
2005, 308 (5725)
:1171-1174

Kustikova, O
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Fehse, B
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Modlich, U
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Yang, M
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Düllmann, J
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Kamino, K
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

von Neuhoff, N
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Schlegelberger, B
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Li, ZX
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany

Baum, C
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Hematol Hemostaseol & Oncol, D-30625 Hannover, Germany
[10]
Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity
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Modlich, Ute
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Bohne, Jens
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Schmidt, Manfred
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von Kalle, Christof
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Knoss, Sabine
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Schambach, Axel
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Baum, Christopher
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BLOOD,
2006, 108 (08)
:2545-2553

Modlich, Ute
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany

Bohne, Jens
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany

Schmidt, Manfred
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany

von Kalle, Christof
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany

Knoss, Sabine
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany

Schambach, Axel
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany

Baum, Christopher
论文数: 0 引用数: 0
h-index: 0
机构: Hannover Med Sch, Dept Expt Hematol, D-30625 Hannover, Germany