[1] Univ Hosp, Dept Med, Tamarac, FL USA
[2] Childrens Mem Hosp, Dept Pediat, Chicago, IL 60614 USA
[3] NW Univ, Sch Med, Chicago, IL USA
[4] Tulane Univ, Sch Med, Hayward Genet Ctr, Human Genet Program, New Orleans, LA 70112 USA
[5] Childrens Hosp Philadelphia, Dept Pediat, Philadelphia, PA 19104 USA
[6] Univ Penn, Philadelphia, PA 19104 USA
[7] NYU, Sch Med, Dept Neurol, New York, NY USA
[8] Mt Sinai Sch Med, Dept Genet, New York, NY USA
[9] Cedars Sinai Med Ctr, Dept Hematol & Oncol, Los Angeles, CA 90048 USA
[10] Univ Washington, Sch Med, Dept Pediat, Seattle, WA 98195 USA
[11] James Whitcomb Riley Hosp Children, Dept Pediat, Indianapolis, IN 46202 USA
[12] James Whitcomb Riley Hosp Children, Dept Med & Mol Genet, Indianapolis, IN 46202 USA
[13] Indiana Univ, Indianapolis, IN 46204 USA
[14] Shaare Zedek Med Ctr, Dept Med, IL-91000 Jerusalem, Israel
[15] Shaare Zedek Med Ctr, Gaucher Clin, Jerusalem, Israel