Clinical findings of a myoclonus-dystonia family with two distinct mutations

被引:44
作者
Doheny, D
Danisi, F
Smith, C
Morrison, C
Velickovic, M
de Leon, D
Bressman, SB
Leung, J
Ozelius, L
Klein, C
Breakefield, XO
Brin, MF
Silverman, JM
机构
[1] Mt Sinai Sch Med, Dept Neurol, New York, NY 10029 USA
[2] Beth Israel Deaconess Med Ctr, Dept Neurol, New York, NY 10003 USA
[3] Massachusetts Gen Hosp, Dept Neurol, Charlestown, MA USA
[4] Harvard Univ, Sch Med, Charlestown, MA USA
[5] Albert Einstein Coll Med, Dept Mol Genet, Bronx, NY 10467 USA
[6] Med Univ Lubeck, Dept Neurol, Lubeck, Germany
关键词
D O I
10.1212/WNL.59.8.1244
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
Myoclonus-dystonia has recently been associated with mutations in the epsilon-sarcoglycan gene (SCGE) on 7q21. Previously, the authors reported a patient with myoclonus-dystonia and an 18-bp deletion in the DYT1 gene on 9q34. The authors have now re-evaluated the patient harboring this deletion for mutations in the SGCE gene and identified a missense change. In the current study, the authors describe the clinical details of this family carrying mutations in two different dystonia genes. Further analysis of these mutations separately and together in cell culture and in animal models should clarify their functional consequences.
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页码:1244 / 1246
页数:3
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