Immune responses to recombinant adeno-associated virus vectors: Putting preclinical findings into perspective

被引:13
作者
Flotte, TR
机构
[1] Univ Florida, Dept Pediat, Gainesville, FL 32610 USA
[2] Univ Florida, Powell Gene Therapy Ctr, Gainesville, FL 32610 USA
关键词
D O I
10.1089/1043034041361190
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
引用
收藏
页码:716 / 717
页数:2
相关论文
共 3 条
  • [1] Autoimmune anemia in macaques following erythropoietin gene therapy
    Chenuaud, P
    Larcher, T
    Rabinowitz, JE
    Provost, N
    Cherel, Y
    Casadevall, N
    Samulski, RJ
    Moullier, P
    [J]. BLOOD, 2004, 103 (09) : 3303 - 3304
  • [2] Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors
    Donsante, A
    Vogler, C
    Muzyczka, N
    Crawford, JM
    Barker, J
    Flotte, T
    Campbell-Thompson, M
    Daly, T
    Sands, MS
    [J]. GENE THERAPY, 2001, 8 (17) : 1343 - 1346
  • [3] Erythropoietin gene therapy leads to autoimmune anemia in macaques
    Gao, GP
    Lebherz, C
    Weiner, DJ
    Grant, R
    Calcedo, R
    McCullough, B
    Bagg, A
    Zhang, Y
    Wilson, JM
    [J]. BLOOD, 2004, 103 (09) : 3300 - 3302