Gene therapy

被引：150

作者：

Kay, MA

Liu, DX

Hoogerbrugge, PM

机构：

[1] UNIV PITTSBURGH,DEPT PHARMACEUT SCI,PITTSBURGH,PA 15261

[2] LEIDEN UNIV,DEPT PEDIAT,LEIDEN,NETHERLANDS

来源：

PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA | 1997年 / 94卷 / 24期

关键词：

D O I：

10.1073/pnas.94.24.12744

中图分类号：

O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];

学科分类号：

07 ; 0710 ; 09 ;

摘要：

In recent years, there have been a number of technological breakthroughs that have allowed for clinical trials in gene therapy to be initiated, In combination,vith the genome initiative, the potential for new therapeutics is limitless, Although an enormous amount of information has been obtained in a relatively short period of time, gene therapy is not get ready for wide-scale practice, Some of the successes and obstacles that remain are summarized in this report.

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页码：12744 / 12746

页数：3

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