Therapeutic options for patients with severe β-thalassemia:: The need for globin gene therapy

被引：40

作者：

Sadelain, Michel ^{[1
]}

Boulad, Farid

Galanello, Renzo

Giardina, Patricia

Locatelli, Franco

Maggio, Aurelio

Rivella, Stefano

Riviere, Isabelle

Tisdale, John

机构：

[1] Mem Sloan Kettering Canc Ctr, Dept Med, Gene Transfer & Gene Express Lab, New York, NY 10021 USA

[2] Mem Sloan Kettering Canc Ctr, Immunol Program, New York, NY 10021 USA

[3] Mem Sloan Kettering Canc Ctr, Dept Pediat, New York, NY 10021 USA

[4] Osped Reg Microcitemie, Pediat Clin, I-09121 Cagliari, Italy

[5] Cornell Univ, Weill Med Coll, New York Presbyterian Hosp, Dept Pediat, New York, NY 10021 USA

[6] Univ Pavia, IRCCS, Policlin San Matteo, I-27100 Pavia, Italy

[7] Azienda Osped Vincenzo Cervello, Div Hematol 2, I-90146 Palermo, Italy

[8] Azienda Osped Vincenzo Cervello, Piera Cutino Res Unit, I-90146 Palermo, Italy

[9] Mem Sloan Kettering Canc Ctr, Gene Transfer & Somat Cell Engn Facil, Dept Med, New York, NY 10021 USA

[10] NIDDK, Mol & Clin Hematol Branch, NIH, Bethesda, MD 20892 USA

来源：

HUMAN GENE THERAPY | 2007年 / 18卷 / 01期

关键词：

D O I：

10.1089/hum.2006.151

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

[No abstract available]

引用

页码：1 / 9

页数：9

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