A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

被引：1377

作者：

Hacein-Bey-Abina, S ^{[1
]}

von Kalle, C

Schmidt, M

Le Deist, F

Wulffraat, N

McIntyre, E

Radford, I

Villeval, JL

Fraser, CC

Cavazzana-Calvo, M

Fischer, A

机构：

[1] Necker Univ Hosp, F-75015 Paris, France

[2] Childrens Hosp Res Fdn, Cincinnati, OH 45229 USA

[3] Univ Freiburg, Sch Med, D-79106 Freiburg, Germany

[4] Wilhelmina Childrens Hosp Univ Med Ctr, NL-3508 AB Utrecht, Netherlands

[5] Millennium Pharmaceut, Cambridge, MA 02139 USA

来源：

NEW ENGLAND JOURNAL OF MEDICINE | 2003年 / 348卷 / 03期

关键词：

D O I：

10.1056/NEJM200301163480314

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

收藏

页码：255 / 256

页数：2

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