A CLN5 mutation causing an atypical neuronal ceroid lipofuscinosis of juvenile onset

被引:41
作者
Pineda-Trujillo, N
Cornejo, W
Carrizosa, J
Wheeler, RB
Múnera, S
Valencia, A
Agudelo-Arango, J
Cogollo, A
Anderson, G
Bedoya, G
Mole, SE
Ruíz-Linares, A
机构
[1] UCL, Galton Lab, Dept Biol, London NW1 2HE, England
[2] UCL, Dept Paediat & Child Hlth, London NW1 2HE, England
[3] Univ Antioquia, Fac Med, Medellin, Colombia
[4] Hosp San Vicente Paul, Medellin, Colombia
[5] Inst Seguros Sociales, Cordoba, Argentina
[6] Great Ormond St Hosp Sick Children, Dept Histopathol, London WC1N 3JH, England
关键词
D O I
10.1212/01.WNL.0000151974.44980.F1
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
Three related patients from Colombia presented with a juvenile-onset neuronal ceroid lipofuscinosis. Electron microscopy of one case showed condensed fingerprint profiles, and genetic analyses identified a novel missense mutation in CLN5. The authors demonstrate the existence of pathogenic CLN5 mutations outside northern Europe and that mutations in this gene can lead to an atypical late-onset neuronal ceroid lipofuscinosis disease, in addition to the late infantile form first described in Finland.
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页码:740 / 742
页数:3
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