CLINICAL INVESTIGATION OF DUCHENNE MUSCULAR-DYSTROPHY - A METHODOLOGY FOR THERAPEUTIC TRIALS BASED ON NATURAL-HISTORY CONTROLS

被引：53

作者：

MENDELL, JR

PROVINCE, MA

MOXLEY, RT

GRIGGS, RC

BROOKE, MH

FENICHEL, GM

MILLER, JP

KAISER, KK

KING, W

ROBISON, J

SIGNORE, L

PANDYA, S

FLORENCE, JM

SEYFRIED, W

MANDEL, S

机构：

[1] UNIV ROCHESTER, STRONG MEM HOSP, ROCHESTER, NY 14642 USA

[2] WASHINGTON UNIV, SCH MED, IRENE WALTER JOHNSON INST REHABIL, DEPT NEUROL & NEUROSURG, ST LOUIS, MO 63110 USA

[3] VANDERBILT UNIV, DEPT NEUROL, NASHVILLE, TN 37240 USA

来源：

ARCHIVES OF NEUROLOGY | 1987年 / 44卷 / 08期

关键词：

D O I：

10.1001/archneur.1987.00520200012009

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：808 / 811

页数：4

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