HEMATOPOIETIC STEM-CELL GENE REPLACEMENT THERAPY

被引:10
作者
KRAUSS, JC
机构
[1] Internal Medicine, The University of Michigan, Ann Arbor, MI
基金
美国国家卫生研究院;
关键词
D O I
10.1016/0304-419X(92)90015-Q
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
[No abstract available]
引用
收藏
页码:193 / 207
页数:15
相关论文
共 97 条
[1]   HUMAN DYSTROPHIN EXPRESSION IN MDX MICE AFTER INTRAMUSCULAR INJECTION OF DNA CONSTRUCTS [J].
ACSADI, G ;
DICKSON, G ;
LOVE, DR ;
JANI, A ;
WALSH, FS ;
GURUSINGHE, A ;
WOLFF, JA ;
DAVIES, KE .
NATURE, 1991, 352 (6338) :815-818
[2]   INTERNAL INITIATION OF TRANSLATION IN RETROVIRAL VECTORS CARRYING PICORNAVIRUS-5' NONTRANSLATED REGIONS [J].
ADAM, MA ;
RAMESH, N ;
MILLER, AD ;
OSBORNE, WRA .
JOURNAL OF VIROLOGY, 1991, 65 (09) :4985-4990
[3]   IDENTIFICATION OF A SIGNAL IN A MURINE RETROVIRUS THAT IS SUFFICIENT FOR PACKAGING OF NONRETROVIRAL RNA INTO VIRIONS [J].
ADAM, MA ;
MILLER, AD .
JOURNAL OF VIROLOGY, 1988, 62 (10) :3802-3806
[4]   HUMAN GENE-THERAPY [J].
ANDERSON, WF .
SCIENCE, 1992, 256 (5058) :808-813
[5]  
[Anonymous], 1991, HUM GENE THER, V2, P251
[6]   EFFECT OF INTERNAL VIRAL SEQUENCES ON THE UTILITY OF RETROVIRAL VECTORS [J].
ARMENTANO, D ;
YU, SF ;
KANTOFF, PW ;
VONRUDEN, T ;
ANDERSON, WF ;
GILBOA, E .
JOURNAL OF VIROLOGY, 1987, 61 (05) :1647-1650
[7]  
BACH FH, 1968, LANCET, V2, P1364
[8]   EXPRESSION OF HUMAN ADENOSINE-DEAMINASE IN MURINE HEMATOPOIETIC-CELLS [J].
BELMONT, JW ;
MACGREGOR, GR ;
WAGERSMITH, K ;
FLETCHER, FA ;
MOORE, KA ;
HAWKINS, D ;
VILLALON, D ;
CHANG, SMW ;
CASKEY, CT .
MOLECULAR AND CELLULAR BIOLOGY, 1988, 8 (12) :5116-5125
[9]   A MAJORITY OF MICE SHOW LONG-TERM EXPRESSION OF A HUMAN BETA-GLOBIN GENE AFTER RETROVIRUS TRANSFER INTO HEMATOPOIETIC STEM-CELLS [J].
BENDER, MA ;
GELINAS, RE ;
MILLER, AD .
MOLECULAR AND CELLULAR BIOLOGY, 1989, 9 (04) :1426-1434
[10]   EVIDENCE THAT THE PACKAGING SIGNAL OF MOLONEY MURINE LEUKEMIA-VIRUS EXTENDS INTO THE GAG REGION [J].
BENDER, MA ;
PALMER, TD ;
GELINAS, RE ;
MILLER, AD .
JOURNAL OF VIROLOGY, 1987, 61 (05) :1639-1646