CORRECTION OF ADENOSINE-DEAMINASE DEFICIENCY IN CULTURED HUMAN T-CELLS AND B-CELLS BY RETROVIRUS-MEDIATED GENE-TRANSFER

被引:165
作者
KANTOFF, PW
KOHN, DB
MITSUYA, H
ARMENTANO, D
SIEBERG, M
ZWIEBEL, JA
EGLITIS, MA
MCLACHLIN, JR
WIGINTON, DA
HUTTON, JJ
HOROWITZ, SD
GILBOA, E
BLAESE, RM
ANDERSON, WF
机构
[1] NCI,METAB BRANCH,BETHESDA,MD 20892
[2] NCI,CLIN ONCOL PROGRAM,BETHESDA,MD 20892
[3] PRINCETON UNIV,DEPT MOLEC BIOL,PRINCETON,NJ 08544
[4] UNIV CINCINNATI,CHILDRENS HOSP MED CTR,DEPT PEDIAT,CINCINNATI,OH 45229
[5] UNIV WISCONSIN HOSP,DEPT PEDIAT,MADISON,WI 53792
关键词
D O I
10.1073/pnas.83.17.6563
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页码:6563 / 6567
页数:5
相关论文
共 34 条
  • [1] CHARACTERIZATION OF NORMAL AND MUTANT ADENOSINE-DEAMINASE MESSENGER-RNAS BY TRANSLATION AND HYBRIDIZATION TO A CDNA PROBE
    ADRIAN, GS
    WIGINTON, DA
    HUTTON, JJ
    [J]. HUMAN GENETICS, 1984, 68 (02) : 169 - 172
  • [2] STRUCTURE OF ADENOSINE-DEAMINASE MESSENGER-RNAS FROM NORMAL AND ADENOSINE DEAMINASE-DEFICIENT HUMAN CELL-LINES
    ADRIAN, GS
    WIGINTON, DA
    HUTTON, JJ
    [J]. MOLECULAR AND CELLULAR BIOLOGY, 1984, 4 (09) : 1712 - 1717
  • [3] TIGHT-BINDING INHIBITORS .4. INHIBITION OF ADENOSINE DEAMINASES BY VARIOUS INHIBITORS
    AGARWAL, RP
    SPECTOR, T
    PARKS, RE
    [J]. BIOCHEMICAL PHARMACOLOGY, 1977, 26 (05) : 359 - 367
  • [4] PROSPECTS FOR HUMAN-GENE THERAPY
    ANDERSON, WF
    [J]. SCIENCE, 1984, 226 (4673) : 401 - 409
  • [5] DEOXYADENOSINE TRIPHOSPHATE AS A POTENTIALLY TOXIC METABOLITE IN ADENOSINE-DEAMINASE DEFICIENCY
    COHEN, A
    HIRSCHHORN, R
    HOROWITZ, SD
    RUBINSTEIN, A
    POLMAR, SH
    HONG, R
    MARTIN, DW
    [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1978, 75 (01) : 472 - 476
  • [6] COLEMAN MS, 1978, J BIOL CHEM, V253, P1619
  • [7] CHARACTERISTICS OF AN AMINOHYDROLASE DISTINCT FROM ADENOSINE-DEAMINASE IN CULTURED HUMAN-LYMPHOBLASTS
    DADDONA, PE
    KELLEY, WN
    [J]. BIOCHIMICA ET BIOPHYSICA ACTA, 1981, 658 (02) : 280 - 290
  • [8] INTRODUCTION OF A SELECTABLE GENE INTO PRIMITIVE STEM-CELLS CAPABLE OF LONG-TERM RECONSTITUTION OF THE HEMATOPOIETIC SYSTEM OF W/WV MICE
    DICK, JE
    MAGLI, MC
    HUSZAR, D
    PHILLIPS, RA
    BERNSTEIN, A
    [J]. CELL, 1985, 42 (01) : 71 - 79
  • [9] IMMUNOLOGICAL AND BIOCHEMICAL PROFILES IN RESPONSE TO TRANSFUSION THERAPY IN AN ADENOSINE DEAMINASE-DEFICIENT PATIENT WITH SEVERE COMBINED IMMUNODEFICIENCY DISEASE
    DYMINSKI, JW
    DAOUD, A
    LAMPKIN, BC
    LIMOUZE, S
    DONOFRIO, J
    COLEMAN, MS
    HUTTON, JJ
    [J]. CLINICAL IMMUNOLOGY AND IMMUNOPATHOLOGY, 1979, 14 (03): : 307 - 326
  • [10] GENE-EXPRESSION IN MICE AFTER HIGH-EFFICIENCY RETROVIRAL-MEDIATED GENE-TRANSFER
    EGLITIS, MA
    KANTOFF, P
    GILBOA, E
    ANDERSON, WF
    [J]. SCIENCE, 1985, 230 (4732) : 1395 - 1398