REPLACEMENT THERAPY FOR INHERITED ENZYME DEFICIENCY - USE OF PURIFIED CERAMIDETRIHEXOSIDASE IN FABRYS-DISEASE

被引：234

作者：

BRADY, RO ^{[1
]}

TALLMAN, JF ^{[1
]}

JOHNSON, WG ^{[1
]}

GAL, AE ^{[1
]}

LEAHY, WR ^{[1
]}

QUIRK, JM ^{[1
]}

DEKABAN, AS ^{[1
]}

机构：

[1] NINDS,DEV METAB NEUROL BRANCH,BETHESDA,MD 20014

来源：

NEW ENGLAND JOURNAL OF MEDICINE | 1973年 / 289卷 / 01期

关键词：

D O I：

10.1056/NEJM197307052890103

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

收藏

页码：9 / 14

页数：6

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