PRODUCTION OF HUMAN GLUCOCEREBROSIDASE IN MICE AFTER RETROVIRAL GENE-TRANSFER INTO MULTIPOTENTIAL HEMATOPOIETIC PROGENITOR CELLS

被引:45
作者
CORRELL, PH [1 ]
FINK, JK [1 ]
BRADY, RO [1 ]
PERRY, LK [1 ]
KARLSSON, S [1 ]
机构
[1] NINCDS,DEV & METAB NEUROL BRANCH,MOLEC & MED GENET SECT,BLDG 10,ROOM 3D04,BETHESDA,MD 20892
关键词
D O I
10.1073/pnas.86.22.8912
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页码:8912 / 8916
页数:5
相关论文
共 38 条
  • [1] EFFECT OF INTERNAL VIRAL SEQUENCES ON THE UTILITY OF RETROVIRAL VECTORS
    ARMENTANO, D
    YU, SF
    KANTOFF, PW
    VONRUDEN, T
    ANDERSON, WF
    GILBOA, E
    [J]. JOURNAL OF VIROLOGY, 1987, 61 (05) : 1647 - 1650
  • [2] MONOCLONAL-ANTIBODIES AGAINST HUMAN BETA-GLUCOCEREBROSIDASE
    BARNEVELD, RA
    TEGELAERS, FPW
    GINNS, EI
    VISSER, P
    LAANEN, EA
    BRADY, RO
    GALJAARD, H
    BARRANGER, JA
    REUSER, AJJ
    TAGER, JM
    [J]. EUROPEAN JOURNAL OF BIOCHEMISTRY, 1983, 134 (03): : 585 - 589
  • [3] Barranger J. A., 1989, METABOLIC BASIS INHE, P1677
  • [4] COMBINATION OF INTERLEUKIN-3 AND INTERLEUKIN-6 PRESERVES STEM-CELL FUNCTION IN CULTURE AND ENHANCES RETROVIRUS-MEDIATED GENE-TRANSFER INTO HEMATOPOIETIC STEM-CELLS
    BODINE, DM
    KARLSSON, S
    NIENHUIS, AW
    [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1989, 86 (22) : 8897 - 8901
  • [5] METABOLISM OF GLUCOCEREBROSIDES .2. EVIDENCE OF AN ENZYMATIC DEFICIENCY IN GAUCHERS DISEASE
    BRADY, RO
    KANFER, JN
    SHAPIRO, D
    [J]. BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 1965, 18 (02) : 221 - &
  • [6] ISOLATION OF BIOLOGICALLY-ACTIVE RIBONUCLEIC-ACID FROM SOURCES ENRICHED IN RIBONUCLEASE
    CHIRGWIN, JM
    PRZYBYLA, AE
    MACDONALD, RJ
    RUTTER, WJ
    [J]. BIOCHEMISTRY, 1979, 18 (24) : 5294 - 5299
  • [7] SINGLE-STEP METHOD OF RNA ISOLATION BY ACID GUANIDINIUM THIOCYANATE PHENOL CHLOROFORM EXTRACTION
    CHOMCZYNSKI, P
    SACCHI, N
    [J]. ANALYTICAL BIOCHEMISTRY, 1987, 162 (01) : 156 - 159
  • [8] THE MOLECULAR-BIOLOGY OF GAUCHER DISEASE AND THE POTENTIAL FOR GENE-THERAPY
    CHOUDARY, PV
    TSUJI, S
    MARTIN, BM
    GUILD, BC
    MULLIGAN, RC
    MURRAY, GJ
    BARRANGER, JA
    GINNS, EI
    [J]. COLD SPRING HARBOR SYMPOSIA ON QUANTITATIVE BIOLOGY, 1986, 51 : 1047 - 1052
  • [9] INTRODUCTION OF A SELECTABLE GENE INTO PRIMITIVE STEM-CELLS CAPABLE OF LONG-TERM RECONSTITUTION OF THE HEMATOPOIETIC SYSTEM OF W/WV MICE
    DICK, JE
    MAGLI, MC
    HUSZAR, D
    PHILLIPS, RA
    BERNSTEIN, A
    [J]. CELL, 1985, 42 (01) : 71 - 79
  • [10] LINEAGE-SPECIFIC EXPRESSION OF A HUMAN BETA-GLOBIN GENE IN MURINE BONE-MARROW TRANSPLANT RECIPIENTS RECONSTITUTED WITH RETROVIRUS-TRANSDUCED STEM-CELLS
    DZIERZAK, EA
    PAPAYANNOPOULOU, T
    MULLIGAN, RC
    [J]. NATURE, 1988, 331 (6151) : 35 - 41