BONE-MARROW TRANSPLANTATION IN CANINE MUCOPOLYSACCHARIDOSIS-1 - EFFECTS WITHIN THE CENTRAL-NERVOUS-SYSTEM

被引:84
作者
SHULL, RM
HASTINGS, NE
SELCER, RR
JONES, JB
SMITH, JR
CULLEN, WC
CONSTANTOPOULOS, G
机构
[1] UNIV TENNESSEE, MEM RES CTR HOSP, KNOXVILLE, TN 37996 USA
[2] NINCDS, DEV & METAB NEUROL BRANCH, BETHESDA, MD 20892 USA
关键词
D O I
10.1172/JCI112830
中图分类号
R-3 [医学研究方法]; R3 [基础医学];
学科分类号
1001 ;
摘要
引用
收藏
页码:435 / 443
页数:9
相关论文
共 43 条
[1]   DIRECT ENZYME TRANSFER FROM LYMPHOCYTES CORRECTS A LYSOSOMAL STORAGE DISEASE [J].
ABRAHAM, D ;
MUIR, H ;
OLSEN, I ;
WINCHESTER, B .
BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 1985, 129 (02) :417-425
[2]   ELECTRON MICROSCOPY OF 2 CEREBRAL BIOPSIES IN GARGOYLISM [J].
ALEU, FP ;
TERRY, RD ;
ZELLWEGER, H .
JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY, 1965, 24 (02) :304-+
[3]   MARROW TRANSPLANTATION IN GENETIC-DISEASE [J].
BARRANGER, JA .
NEW ENGLAND JOURNAL OF MEDICINE, 1984, 311 (25) :1629-1631
[4]   PLURIPOTENTIAL HEMATOPOIETIC STEM-CELLS IN ADULT-MOUSE BRAIN [J].
BARTLETT, PF .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA-BIOLOGICAL SCIENCES, 1982, 79 (08) :2722-2725
[5]  
BAYEVER E, 1985, LANCET, V2, P471
[6]  
BREEN M, 1976, METHODS CARBOHYDRATE, V7, P101
[7]   NEUROCHEMICAL CHARACTERIZATION OF CANINE ALPHA-L-IDURONIDASE DEFICIENCY DISEASE (MODEL OF HUMAN MUCOPOLYSACCHARIDOSIS-I) [J].
CONSTANTOPOULOS, G ;
SHULL, RM ;
HASTINGS, N ;
NEUFELD, EF .
JOURNAL OF NEUROCHEMISTRY, 1985, 45 (04) :1213-1217
[8]   PARTIAL ENZYME DEFICIENCIES - RESIDUAL ACTIVITIES AND THE DEVELOPMENT OF NEUROLOGICAL DISORDERS [J].
CONZELMANN, E ;
SANDHOFF, K .
DEVELOPMENTAL NEUROSCIENCE, 1984, 6 (01) :58-71
[9]  
DESAI S, 1983, EXP HEMATOL, V11, P98
[10]   SOLITARY CELLS AND ENZYME EXCHANGE IN TETRAPARENTAL MICE [J].
FEDER, N .
NATURE, 1976, 263 (5572) :67-69