The cost of treating Gaucher disease

被引:13
作者
Beutler, E
机构
关键词
D O I
10.1038/nm0596-523
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
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页码:523 / 524
页数:2
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共 8 条
[1]  
BALLCKI D, 1995, MEDICINE, V74, P305
[2]   TREATMENT REGIMENS IN GAUCHERS-DISEASE [J].
BEUTLER, E .
LANCET, 1995, 346 (8974) :581-582
[3]   THE CLINICAL COURSE OF TREATED AND UNTREATED GAUCHER-DISEASE - A STUDY OF 45 PATIENTS [J].
BEUTLER, E ;
DEMINA, A ;
LAUBSCHER, K ;
GARVER, P ;
GELBART, T ;
BALICKI, D ;
VAUGHAN, L .
BLOOD CELLS MOLECULES AND DISEASES, 1995, 21 (02) :86-108
[4]   HCG CONTAMINATION OF ALGLUCERASE - CLINICAL IMPLICATIONS IN LOW-DOSE REGIMEN [J].
COHEN, Y ;
ELSTEIN, D ;
ABRAHAMOV, A ;
HIRSCH, H ;
ZIMRAN, A .
AMERICAN JOURNAL OF HEMATOLOGY, 1994, 47 (03) :235-236
[5]   INDIVIDUALIZED LOW-DOSE ALGLUCERASE THERAPY FOR TYPE-1 GAUCHERS-DISEASE [J].
HOLLAK, CEM ;
AERTS, JMFG ;
GOUDSMIT, R ;
PHOA, SSKS ;
EK, M ;
VANWEELY, S ;
VONDEMBORNE, AEGK ;
VANOERS, MHJ .
LANCET, 1995, 345 (8963) :1474-1478
[6]  
*NATL I HLTH TECHN, 1995, GAUCH DIS CURR ISS D
[7]  
ROBINSON ML, 1996, BIOWORLD TODAY, V7, P1
[8]   LOW-DOSE ENZYME REPLACEMENT THERAPY FOR GAUCHERS-DISEASE - EFFECTS OF AGE, SEX, GENOTYPE, AND CLINICAL-FEATURES ON RESPONSE TO TREATMENT [J].
ZIMRAN, A ;
ELSTEIN, D ;
KANNAI, R ;
ZEVIN, S ;
HADASHALPERN, I ;
LEVYLAHAD, E ;
COHEN, Y ;
HOROWITZ, M .
AMERICAN JOURNAL OF MEDICINE, 1994, 97 (01) :3-13